Status:
UNKNOWN
Identifying Characteristics of Bone Marrow Failure Syndromes
Lead Sponsor:
Office of Rare Diseases (ORD)
Collaborating Sponsors:
Rare Diseases Clinical Research Network
Conditions:
Bone Marrow Failure Syndromes
Anemia, Aplastic
Eligibility:
All Genders
11+ years
Brief Summary
Bone marrow failure syndromes (BMFS) are rare disorders characterized by dysfunctional hematopoietic stem cells, which give rise to all red and white blood cells. The deficiency of blood cells, or cyt...
Detailed Description
BMFS result from hematopoietic progenitor or stem cell failure within the bone marrow. Specific causes of this problem, however, have been difficult to identify, as BMFS occur sporadically. For the sa...
Eligibility Criteria
Inclusion
- Diagnosis of one of the following diseases: aplastic anemia; myelodysplastic syndrome; paroxysmal nocturnal hemoglobinuria; idiopathic pure red cell aplasia; amegakaryocytic thrombocytopenia purpura; or large granular lymphocyte leukemia
Exclusion
- N/A
Key Trial Info
Start Date :
April 1 2006
Trial Type :
OBSERVATIONAL
Allocation :
ESTIMATED
End Date :
July 1 2009
Estimated Enrollment :
450 Patients enrolled
Trial Details
Trial ID
NCT00315419
Start Date
April 1 2006
End Date
July 1 2009
Last Update
April 21 2010
Active Locations (4)
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1
University of California, Los Angeles, Department of Hematology and Oncology
Los Angeles, California, United States, 90095
2
H. Lee Moffitt Cancer Center
Tampa, Florida, United States, 33612
3
Cleveland Clinic Foundation
Cleveland, Ohio, United States, 44195
4
Pennsylvania State University Cancer Center
Hershey, Pennsylvania, United States, 17033