Status:

TERMINATED

Phase 2, Open-Label, Multi-Dose Study of Panhematin in Patients With MDS

Lead Sponsor:

Rush University Medical Center

Collaborating Sponsors:

H. Lundbeck A/S

Conditions:

Myelodysplastic Syndrome

Eligibility:

All Genders

18+ years

Phase:

PHASE2

Brief Summary

This is a Phase II, open-label clinical trial examining the role of Panhematin® in patients with MDS. The objective of this study is to evaluate the safety and efficacy of Panhematin® (hematin for inj...

Detailed Description

The myelodysplastic syndromes (MDS), a diverse group of hematopoietic stem cell (HSC) disorders, are characterized by ineffective hematopoiesis that manifest clinically as anemia, neutropenia, and/or ...

Eligibility Criteria

Inclusion

  • A patient will be eligible for study participation if all of the following criteria are met:
  • The patient must sign and date the IRB/IEC approved Informed Consent Form/HIPAA Authorization prior to study participation.
  • Patient is at least 18 years of age.
  • If female:
  • Patient, either male or female, is either not of childbearing potential, defined as postmenopausal for at least 1 year or surgically sterile (bilateral tubal ligation, bilateral oophorectomy or hysterectomy), or if of childbearing potential, must comply with an effective method of birth control acceptable to the Investigator during the study (oral contraceptives, Depo-Provera, intra-uterine device), for at least 1 month prior to enrollment and for 1 month following the completion of the study.
  • Patient is not breastfeeding.
  • Patient of childbearing potential must have a negative urine or serum pregnancy test during the screening period.
  • Patient has a diagnosis of low- or intermediate-1 risk MDS, as determined by the International Prognostic Scoring (IPSS) (score of 0-1).
  • Patient must be transfusion dependent (i.e., received ≥ 2 units over an 8-week period prior to registration) or have a hemoglobin value ≤ 10 g/dL on the screening laboratories.
  • Patients must have ≤ 10% blasts in the bone marrow and peripheral blood.
  • Patient must have a platelet counts \> 50,000/microliters and absolute neutrophil counts (ANC) \>500/microliters.
  • Patient must have adequate hepatic and renal functions, defined as serum bilirubin, serum glutamic-oxaloacetic transaminase (SGOT), and serum glutamate pyruvate transaminase (SGPT) ≤ 2 times the upper limit of normal (ULN), and creatinine ≤ 1.5 times the ULN.
  • Patient must have an ECOG score of ≤ 2.
  • The patient has a negative human immunodeficiency virus antibody (HIV) test result.

Exclusion

  • A patient will be ineligible for study participation if any of the following criteria are met:
  • The patient has a history of an allergic reaction or significant sensitivity to Panhematin®.
  • The patient has taken or used any investigational drug or device in the 30 days prior to screening.
  • The patient has chronic myelomonocytic leukemia (CMML).
  • The patient has a history of deep vein thrombosis or known hypercoagulable state.
  • The patient has a history of a pre-existing medical condition that, in the opinion of the investigator, will interfere with the participation in the study.
  • The patient has poor peripheral venous access, if central venous access is not available.
  • The patient has an uncontrolled active infection.
  • The patient has positive test results for hepatitis B surface antigen, and hepatitis C virus antibody.
  • The patient has any other condition or prior therapy that, in the opinion of the Investigator, would make the patient unsuitable for the study.

Key Trial Info

Start Date :

May 1 2007

Trial Type :

INTERVENTIONAL

Allocation :

ACTUAL

End Date :

January 1 2009

Estimated Enrollment :

6 Patients enrolled

Trial Details

Trial ID

NCT00467610

Start Date

May 1 2007

End Date

January 1 2009

Last Update

October 24 2014

Active Locations (1)

Enter a location and click search to find clinical trials sorted by distance.

Page 1 of 1 (1 locations)

1

Rush University Medical Center

Chicago, Illinois, United States, 60612