Status:

COMPLETED

Oral LGD-4665 Versus Placebo in Adults With Immune Thrombocytopenic Purpura (ITP) for 6 Weeks Plus Open Treatment Continuation

Lead Sponsor:

GlaxoSmithKline

Conditions:

Immune Thrombocytopenic Purpura

Eligibility:

All Genders

18+ years

Phase:

PHASE2

Brief Summary

The purpose of this study is to assess the ability of LGD-4665 given daily by mouth to increase platelet counts in the treatment of patients with ITP (immune thrombocytopenic purpura). LGD-4665 increa...

Detailed Description

This is a Phase IIA study with two parts to the design. * Part 1 is a randomized, double-blinded, placebo-controlled treatment of 7.5 mg/day LGD-4665 versus placebo in approximately 24 patients with ...

Eligibility Criteria

Inclusion

  • Inclusion Criteria:
  • Adults 18 years or older
  • Diagnosis of ITP for at least 3 months consistent with ASH guidelines
  • Treated with one or more prior therapies for ITP and platelet counts \< 30,000/µL or \< 50,000/µL if on a stable oral corticosteroid for ≥ 4 weeks, supported by 2 platelet counts in prior 30 days
  • Laboratory results within normal range except for the following analytes
  • Hemoglobin ≥ 10 g/dL
  • Absolute neutrophil counts \> 1000/mL
  • ALT ≤ 1.5X ULN
  • AST ≤ 1.5X ULN
  • Creatinine \< 1.5X ULN
  • Bilirubin \< 1.5X ULN
  • BUN \< 1.5X ULN
  • PT \< 1.5X ULN
  • aPTT \<1.5X ULN
  • Women of child-bearing potential must have a negative serum pregnancy test within 4 days prior to the first dose of study treatment and agree to practice an approved method of contraception or abstinence from sexual intercourse.
  • Willing to sign a written informed consent
  • Exclusion criteria:
  • History of heart attack or cardiovascular disease
  • Known history of arterial or venous thrombosis
  • More than 3 risk factors for thromboembolic events (diabetes, smoker, using oral contraception, using estrogen therapy, hypertriglyceridemia, average cholesterol \> 240 mg/dL, treatment for hypertension)
  • Active cancer or a history of bone marrow disorders
  • Women who are pregnant or nursing
  • History of alcohol/drug abuse or dependence within one year
  • Listed medications dosed within:
  • 4 weeks of the first dose of the study treatment:
  • Use of Rituximab
  • Use of cytotoxic agents
  • Use of Cyclosporine and other immunomodulators
  • Use of an investigational drug
  • 2 weeks of the first dose of the study treatment:
  • Use of Danazol
  • Use of Azathioprine
  • Use of Mycophenolate mofetil and pulsed-dose steroids
  • 1 week of the first dose of the study treatment:
  • Use of Anti-D (WinRho®)
  • Use of IVIG
  • Had a platelet transfusion
  • Use of herbal/dietary supplements (excluding vitamins and mineral supplements)
  • 3 days of the first dose of the study treatment
  • Use of aspirin, aspirin containing compounds
  • salicylates
  • milk of magnesia
  • non-steroidal anti-inflammatory drugs (unless prescribed for heart disease)
  • History of platelet aggregation that would prevent measurement of platelet counts
  • Known active infection with HIV, hepatitis B, or hepatitis C
  • In the Investigator's opinion, the patient is not able to comply with requirements of the study

Exclusion

    Key Trial Info

    Start Date :

    March 15 2008

    Trial Type :

    INTERVENTIONAL

    Allocation :

    ACTUAL

    End Date :

    May 15 2009

    Estimated Enrollment :

    23 Patients enrolled

    Trial Details

    Trial ID

    NCT00621894

    Start Date

    March 15 2008

    End Date

    May 15 2009

    Last Update

    December 16 2024

    Active Locations (15)

    Enter a location and click search to find clinical trials sorted by distance.

    Page 1 of 4 (15 locations)

    1

    University of California San Diego Medical Center

    San Diego, California, United States, 92103-8409

    2

    University of California, San Francisco

    San Francisco, California, United States, 94143-1270

    3

    Davis, Posteraro and Wasser, MD's LLP

    Manchester, Connecticut, United States, 06040

    4

    Baptist Cancer Institute

    Jacksonville, Florida, United States, 32207