Status:

TERMINATED

RAD001(Everolimus) in Treating Patients With Myelodysplastic Syndromes

Lead Sponsor:

Case Comprehensive Cancer Center

Collaborating Sponsors:

National Cancer Institute (NCI)

Conditions:

Myelodysplastic Syndromes

Eligibility:

All Genders

18+ years

Phase:

PHASE2

Brief Summary

RATIONALE: RAD001(Everolimus) may stop the growth of cancer cells by blocking some of the enzymes needed for their growth and by blocking blood flow to the cancer. PURPOSE: This phase II trial is stu...

Detailed Description

OBJECTIVES: Primary * Determine the clinical activity (improvement in erythroid response and/or improvement in other cytopenias, bone marrow morphology/cytogenetics) of RAD001(everolimus) in patient...

Eligibility Criteria

Inclusion

  • DISEASE CHARACTERISTICS:
  • Low or intermediate-1 risk myelodysplastic syndromes by International Prognostic Scoring System (IPSS) criteria
  • IPSS score \< 1.5
  • Requiring transfusion of 2 units of red blood cells at least once a month (four weeks prior to accrual on study)
  • High levels of endogenous epoetin alfa (i.e., \> 200 mU/mL)
  • Unlikely to respond to epoetin alfa, or has a documented clinical non-response to epoetin alfa (at a dose of ≥ 40,000 U weekly) or darbepoetin alfa (at a dose \> 200 mcg every other week) (i.e., \< 2 g/dL increase in hemoglobin and no decrease in transfusion requirements after at least 4 weeks of treatment)
  • No chronic myelomonocytic leukemia
  • PATIENT CHARACTERISTICS:
  • ECOG Performance Status of 0-2
  • Liver enzymes (AST and ALT) and total bilirubin ≤ 2 times upper limit of normal
  • Serum creatinine ≤ 2 times upper limits of normal
  • No clinically significant anemia due to iron, B12, or folate deficiencies; autoimmune or hereditary hemolysis; or gastrointestinal bleeding
  • Not pregnant or nursing
  • Negative pregnancy test
  • Fertile patients must use effective contraception
  • No other serious or poorly controlled medical condition that could be exacerbated by or complicate compliance with study therapy
  • PRIOR CONCURRENT THERAPY:
  • At least 4 weeks since prior treatment (including growth factors)
  • No chronic use (\> 2 weeks) of physiologic doses of a corticosteroid agent (dose equivalent to \> 10 mg/day of prednisone) within 28 days of the first day of study drug
  • No concurrent use of another investigational agent
  • No concurrent therapy with any cytotoxic drugs, steroids, or growth factors

Exclusion

    Key Trial Info

    Start Date :

    November 1 2005

    Trial Type :

    INTERVENTIONAL

    Allocation :

    ACTUAL

    End Date :

    March 1 2009

    Estimated Enrollment :

    7 Patients enrolled

    Trial Details

    Trial ID

    NCT00809185

    Start Date

    November 1 2005

    End Date

    March 1 2009

    Last Update

    March 7 2019

    Active Locations (1)

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    Cleveland Clinic Taussig Cancer Institute, Case Comprehensive Cancer Center

    Cleveland, Ohio, United States, 44195