Status:

COMPLETED

A Study of the Use of Factor XIII Concentrate in Patients With Inherited FXIII Deficiency

Lead Sponsor:

CSL Behring

Conditions:

Factor XIII Deficiency

Eligibility:

All Genders

Phase:

PHASE2

Brief Summary

Congenital deficiency of Factor XIII is an extremely rare hereditary disorder associated with potentially life-threatening bleeding. This study will evaluate the safety and recommended (best) amount o...

Eligibility Criteria

Inclusion

  • Written informed consent/assent for study participation obtained before undergoing any study-specific procedures
  • Documented congenital FXIII deficiency that requires prophylactic treatment with a FXIII containing product.
  • Males and females of any age with congenital FXIII deficiency.
  • Received full hepatitis B vaccination and/or is hepatitis B surface antibody positive

Exclusion

  • Diagnosis of acquired FXIII deficiency
  • Administration of a FXIII-containing product, including blood transfusions or other blood products within 4 weeks prior to the planned Day 0
  • Any known congenital or acquired coagulation disorder other than congenital FXIII deficiency
  • Known or suspected to have antibodies towards FXIII
  • Use of any other investigational medicinal product within 4 weeks prior to the Baseline Visit (Day 0)
  • Positive result at screening for human immunodeficiency virus (HIV)
  • Serum aspartate transaminase (AST) or serum alanine transaminase (ALT) concentration \>2.5 times the upper limit of normal
  • Fibrinogen \< lower limit of normal
  • Active bleeding
  • Pregnant or breast-feeding
  • Intention to become pregnant during the course of the study
  • Female subjects of childbearing potential not using, or not willing to use, a medically reliable method of contraception for the entire duration of the study
  • Surgical procedure anticipated during the study period
  • Suspected inability (e.g., language problems) or unwillingness to comply with study procedures or history of noncompliance

Key Trial Info

Start Date :

May 1 2009

Trial Type :

INTERVENTIONAL

Allocation :

ACTUAL

End Date :

April 1 2010

Estimated Enrollment :

15 Patients enrolled

Trial Details

Trial ID

NCT00883090

Start Date

May 1 2009

End Date

April 1 2010

Last Update

January 16 2012

Active Locations (6)

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Page 1 of 2 (6 locations)

1

Study Site

Dothan, Alabama, United States, 36305

2

Study Site

Orange, California, United States, 92868

3

Study Site

San Francisco, California, United States, 94115

4

Study Site

Stockton, California, United States, 95204