Status:

COMPLETED

The Effect of Diflunisal on Familial Transthyretin Amyloidosis

Lead Sponsor:

Umeå University

Conditions:

Amyloidosis

Eligibility:

All Genders

18+ years

Brief Summary

An ongoing trial of diflunisal has been closed for enrollment, thus, patients suitable for the study can no longer participate or receive treatment by diflunisal; and patients, who have participated i...

Detailed Description

Duration of treatment in this study is dependent of the results from the ongoing IND 68092-study, which are planned to be presented 2013.

Eligibility Criteria

Inclusion

  • Biopsy and genetically proven systemic transthyretin amyloidosis caused by a TTR gene mutation. The amyloid shall be proven to be of transthyretin type, and the fibril composition settled.
  • Age ≥ 18 years.
  • Negative pregnancy test and contraception for sexually active women of child bearing potential.

Exclusion

  • Concomitant use of non-study non-steroidal anti-inflammatory drugs (NSAIDs)
  • Heart failure with symptoms at daily activities (NYHA class ≥III)
  • Renal insufficiency (creatinine clearance \< 30 ml calculated from the Cockcroft-Gault formula)
  • Active non-haemorrhoidal bleeding within the last 18 month.
  • Non-treated peptic ulcer disease.
  • Anticoagulation therapy, low dose ASA permitted.
  • Non-steroidal or aspirin allergy/hypersensitivity
  • Thrombocytopenia (\< 100,000 platelets/mm3)
  • Inability or unwillingness of subject to give written informed consent
  • By the investigator regarded as unable to follow the study guidelines and scheduled controls.

Key Trial Info

Start Date :

August 1 2011

Trial Type :

OBSERVATIONAL

Allocation :

ACTUAL

End Date :

December 1 2014

Estimated Enrollment :

55 Patients enrolled

Trial Details

Trial ID

NCT01432587

Start Date

August 1 2011

End Date

December 1 2014

Last Update

August 24 2015

Active Locations (3)

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Page 1 of 1 (3 locations)

1

Dept of Clinical Medicin, Ptieå Hospital

Piteå, Sweden, SE-941 28

2

Dept of clinical medicin, Skellefteå Hospital

Skellefteå, Sweden, SE-931 86

3

Dept of Clinical Medicine, Umeå University Hospital

Umeå, Sweden, SE-90185