Status:

COMPLETED

Efficacy, Safety and Tolerability of Icatibant for the Treatment of HAE

Lead Sponsor:

Massachusetts General Hospital

Collaborating Sponsors:

Shire Human Genetic Therapies, Inc.

Conditions:

Hereditary Angioedema

Eligibility:

All Genders

18+ years

Phase:

PHASE4

Brief Summary

The investigators propose a study to evaluate the safety, local tolerability, convenience, and efficacy of self-administered Icatibant for the treatment of acute attacks of hereditary angioedema. The ...

Eligibility Criteria

Inclusion

  • Males and females at least 18 years of age at the time of informed consent
  • Documented diagnosis of hereditary angioedema Type I or II based on ALL of the following criteria:
  • Family and/or medical history
  • Characteristic attack manifestations, recurrent attacks
  • Historical low C4, normal C1q and either low C1-INH or low C1INH function
  • Women of childbearing potential must use consistently and correctly a highly effective, adequate method of birth control (failure rate less than 1% per year), sexual abstinence or have a vasectomised partner during the duration of the study. Hormonal contraception can be continued if verified by a physician that it doesn't affect the course of hereditary angioedema attacks.
  • Mental and physical condition allowing patients to complete baseline assessment, to self-administer Icatibant and to follow other study procedures.
  • Ability to provide signed written informed consent after all aspects of the study have been explained and discussed with the patient.

Exclusion

  • Participation in a clinical therapeutic trial of another investigational medicinal product within the past month (except a previous Icatibant study).
  • Diagnosis of angioedema other than Type I or Type II hereditary angioedema.
  • Evidence of symptomatic coronary artery disease based on medical history, in particular, unstable angina pectoris or severe coronary heart disease.
  • Congestive heart failure (NYHA Class 3 and 4).
  • Stroke within the past 6 months.
  • Treatment with angiotensin converting enzyme inhibitor.
  • Pregnancy and/or breast-feeding.
  • In the opinion of the investigator: mental condition rendering the patient unable to understand the nature, scope and possible consequences of the study.
  • In the opinion of the investigator: unlikely to comply with the protocol, for example, uncooperative attitude, inability to return for follow-up visits, or unlikely to complete the study for any reason.
  • In the opinion of the investigator: inability to complete the patient diary, manage study medication or self-administration of an injection.

Key Trial Info

Start Date :

December 1 2011

Trial Type :

INTERVENTIONAL

Allocation :

ACTUAL

End Date :

April 1 2014

Estimated Enrollment :

19 Patients enrolled

Trial Details

Trial ID

NCT01457430

Start Date

December 1 2011

End Date

April 1 2014

Last Update

October 18 2016

Active Locations (5)

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Page 1 of 2 (5 locations)

1

San Diego Veterans Affairs Medical Center

La Jolla, California, United States

2

UCLA - David Geffen School of Medicine

Los Angeles, California, United States

3

Institute for Allergy and Asthma

Wheaton, Maryland, United States, 20902

4

Penn State University

Hershey, Pennsylvania, United States, 17033