Status:

COMPLETED

Study of the Combination of Panobinostat and Carfilzomib in Patients With Relapsed/Refractory Multiple Myeloma

Lead Sponsor:

SCRI Development Innovations, LLC

Collaborating Sponsors:

Onyx Therapeutics, Inc.

Novartis

Conditions:

Multiple Myeloma

Eligibility:

All Genders

18+ years

Phase:

PHASE1

PHASE2

Brief Summary

Relapsed/refractory Multiple Myeloma (MM) is an incurable disorder with a poor prognosis. Carfilzomib is a novel proteasome inhibitor with activity in this setting. Panobinostat is a pan-deacetylase i...

Detailed Description

In this open-label, non-randomized Phase I/II study, a maximum of 4 planned dose levels of carfilzomib and panobinostat were evaluated to determine the maximum tolerated dose (MTD) to administer. The ...

Eligibility Criteria

Inclusion

  • Eligible participants must have multiple myeloma using standard criteria.
  • Patients must have measurable disease requiring systemic therapy defined as at least one of the following:
  • Serum M-protein ≥1 g/dl (≥10 g/l)
  • Urine M-protein ≥200 mg/24 hrs
  • Serum free light chain assay: involved free light chain level ≥10 mg/dl (≥100 mg/l) provided the serum free light chain ratio is abnormal
  • Must have progressed during or after at least one previous bortezomib-containing treatment regimen. Patients who have received previous high-dose therapy/autologous stem cell transplantation are eligible.
  • Eastern Cooperative Oncology Group (ECOG) performance status of 0-2.
  • Must meet the following laboratory criteria:
  • Absolute neutrophil count (ANC) ≥1000/μL;
  • Platelets ≥70,000/microL;
  • AST or ALT and alkaline phosphatase (ALP) must be ≤ 2.5 x ULN, or ≤ 5 x ULN in patients with plasmacytomas of the liver;
  • Total bilirubin ≤ 1.5 x the institutional ULN;
  • Serum creatinine ≤ 1.5 x ULN or calculated creatinine clearance ≥ 50 ml/min;
  • Serum potassium, calcium, magnesium WNL (These may be corrected prior to starting therapy, to make the patient eligible.)
  • Ability to swallow oral medications.
  • Baseline MUGA or ECHO must demonstrate left ventricular ejection fraction (LVEF) ≥ the lower limit of the institutional limits of normal.
  • Male or females ≥ 18 years of age.
  • Female patients must not be of child-bearing potential or must agree to use adequate contraceptive measures.
  • Male patients willing to use adequate contraceptive measures.
  • Willingness and ability to comply with the trial and follow-up procedures.
  • Ability to understand the nature of this trial and give written informed consent.

Exclusion

  • Currently receiving or have received systemic cancer therapy (chemotherapy, biologic therapy) ≤ 21 days of initiating study therapy. For patients receiving small molecule targeted therapy, study treatment may begin \>21 days after last dose or \>5 half lives of previous treatment, whichever is shorter. Patients must have completed radiation therapy ≥7 days prior to starting study treatment. Patients must have recovered from or come to a new chronic stable baseline from all treatment-related toxicities. Dexamethasone or other high-dose steroid therapy must be stopped ≥ days prior to starting study treatment.
  • Previous treatment with HDAC, DAC, HSP90 or valproic acid for treatment of cancer.
  • Requires valproic acid for any medical condition during the study ≤5 days prior to first panobinostat treatment.
  • Patient has not recovered from all therapy-related toxicities associated with prior treatments to \< Grade 2 CTCAE.
  • Known history of allergy to Captisol® (a cyclodextrin derivative used to solubilize carfilzomib).
  • Patients with pleural effusions requiring thoracentesis or ascites requiring paracentesis ≤14 days prior to study entry.
  • Patients using medications that have a risk of prolonging the QT interval or inducing Torsade de Pointes if treatment cannot be discontinued or switched to a different medication prior to receiving study drug.
  • Patients with \> grade 2 diarrhea.
  • Patients with impaired cardiac function.
  • Infection requiring IV antibiotics.
  • Patients with \> grade 2 peripheral neuropathy or with uncontrolled pain.
  • Women who are pregnant or lactating.
  • Any concurrent medical illness that may impair the ability of the patient to tolerate study treatment and comply with the requirements of the study.
  • Mental condition that would prevent patient comprehension of the nature of, and risk associated with, the study.
  • Use of any non-approved or investigational agent ≤30 days prior to administration of the first dose of study drug. Patients may not receive any other investigational or anti-cancer treatments while participating in this study.
  • Presence of other active cancers, or history of treatment for invasive cancer ≤ 5 years. Patients with stage I cancer who have received definitive local treatment at least 3 years previously, and are considered unlikely to recur are eligible. All patients with previously treated in situ carcinoma (i.e. non-invasive) are eligible, as are patients with history of non-melanoma skin cancer.

Key Trial Info

Start Date :

December 1 2011

Trial Type :

INTERVENTIONAL

Allocation :

ACTUAL

End Date :

December 1 2020

Estimated Enrollment :

80 Patients enrolled

Trial Details

Trial ID

NCT01496118

Start Date

December 1 2011

End Date

December 1 2020

Last Update

February 2 2022

Active Locations (13)

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Page 1 of 4 (13 locations)

1

Colorado Blood Cancer Institute

Denver, Colorado, United States, 80218

2

Florida Cancer Specialists South

Fort Myers, Florida, United States, 33916

3

Woodlands Medical Specialists

Pensacola, Florida, United States, 32503

4

Florida Cancer Specialists North

St. Petersburg, Florida, United States, 33705