Status:

TERMINATED

Safety Study of PLX-PAD Cells to Treat Pulmonary Arterial Hypertension (PAH)

Lead Sponsor:

United Therapeutics

Conditions:

Pulmonary Arterial Hypertension

Eligibility:

All Genders

18-75 years

Phase:

PHASE1

Brief Summary

The purpose of this clinical study is to assess the safety of PLX-PAD to treat pulmonary arterial hypertension (PAH). PLX-PAD is a cell-based product made of allogeneic Mesenchymal-like Adherent Strom...

Eligibility Criteria

Inclusion

  • Summary of inclusion and exclusion criteria.
  • Eligible subjects:
  • Are between 18 and 75 years of age
  • Have a minimum weight of 45 kg
  • Have a diagnosis of idiopathic or heritable PAH, PAH associated with connective tissue disease (CTD), PAH associated with repaired congenital systemic-to-pulmonary cardiac shunt (at least one year since repair), or PAH associated with appetite suppressant/drug or toxin use confirmed by RHC
  • Have a current WHO functional class II or III designation
  • Have been stabilized, without dose changes for at least 30 days prior to the Screening visit on at least two approved PAH medications (e.g., PDE-5 inhibitor, ERA, prostanoid \[as inhalation or infusion\]); or IV prostanoid monotherapy. Subjects on an IV prostanoid must have been receiving therapy for at least three months prior to the Screening visit.
  • Have a 6MWD equal to or greater than 200 meters (m) at the Screening and Baseline Visits.
  • Subjects must not:
  • Have any evidence of pulmonary thrombus, significant coronary artery disease (CAD), left ventricular dysfunction, or a restrictive or congestive cardiomyopathy
  • Have a history of malignancies within the past 5 years,with the exception of individuals with localized, non-metastatic basal cell carcinoma of the skin, in situ carcinoma of the cervix, or prostate cancer who are not currently or expected to undergo radiation therapy, chemotherapy and/or surgical intervention, or to initiate hormonal treatment during the study
  • Be listed for transplantation
  • Be pregnant or nursing

Exclusion

    Key Trial Info

    Start Date :

    April 1 2013

    Trial Type :

    INTERVENTIONAL

    Allocation :

    ACTUAL

    End Date :

    January 1 2016

    Estimated Enrollment :

    6 Patients enrolled

    Trial Details

    Trial ID

    NCT01795950

    Start Date

    April 1 2013

    End Date

    January 1 2016

    Last Update

    February 17 2016

    Active Locations (2)

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    Page 1 of 1 (2 locations)

    1

    The Prince Charles Hospital

    Brisbane, Queensland, Australia, 4032

    2

    The Alfred Hospital

    Melbourne, Australia