Status:

RECRUITING

Immune Disorder HSCT Protocol

Lead Sponsor:

Washington University School of Medicine

Conditions:

Immune Deficiency Disorders

Severe Combined Immunodeficiency

Eligibility:

All Genders

Up to 21 years

Phase:

PHASE2

Brief Summary

This study hypothesizes that a reduced intensity immunosuppressive preparative regimen will establish engraftment of donor hematopoietic cells with acceptable early and delayed toxicity in patients wi...

Eligibility Criteria

Inclusion

  • \</= 28 years of age
  • Performance status \>/= 40
  • DLCO \>/= 40%
  • LVEF \>/=40% or LVSF \>/=26%
  • Serum creatinine \< 2x ULN
  • Liver enzymes \</= 5x ULN
  • Negative pregnancy test
  • Suitably matched donor (6/6 matched sib UCB, 8/8 matched sib BM or PBSC, 5-6/6 matched unrelated UCB, 7-8/8 matched unrelated BM, double cord)

Exclusion

  • Known diagnosis of HIV I/II
  • Pregnant or breastfeeding
  • Uncontrolled invasive fungal or bacterial infections within 1 month prior to starting alemtuzumab
  • Uncontrolled viral infection within 1 week prior to starting alemtuzumab

Key Trial Info

Start Date :

March 1 2013

Trial Type :

INTERVENTIONAL

Allocation :

ESTIMATED

End Date :

March 1 2027

Estimated Enrollment :

20 Patients enrolled

Trial Details

Trial ID

NCT01821781

Start Date

March 1 2013

End Date

March 1 2027

Last Update

July 3 2024

Active Locations (1)

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1

Washington University

St Louis, Missouri, United States, 63110