Status:

COMPLETED

Pharmacokinetic/Pharmacodynamic Study of Udenafil in Adolescents

Lead Sponsor:

Mezzion Pharma Co. Ltd

Collaborating Sponsors:

National Heart, Lung, and Blood Institute (NHLBI)

Pediatric Heart Network

Conditions:

Single Ventricle Heart Disease After Fontan Surgery

Eligibility:

All Genders

14-18 years

Phase:

PHASE1

PHASE2

Brief Summary

To determine the pharmacokinetic profile and safety of udenafil in adolescents with Fontan physiology and to assess the short-term pharmacodynamic effect of udenafil on pharmacodynamic measures of exe...

Detailed Description

A dose escalation trial to determine the pharmacokinetics, safety and tolerance of udenafil in male and female adolescent subjects with single ventricle physiology that that have undergone the Fontan ...

Eligibility Criteria

Inclusion

  • Males and females with Fontan physiology who are 14-18 years of age.
  • Willingness to return to center to complete blood draws and exercise tests as described in the study protocol.
  • Patients must agree to abstain from alcohol, caffeinated beverages, and grapefruit juice for the duration of the trial.
  • Informed assent from subject informed consent from parent/legal guardian as appropriate.

Exclusion

  • Non-cardiac medical, psychiatric, and/or social disorder that would prevent successful completion of planned study testing or would invalidate its results.
  • Height \<132 cm (minimum height requirement for exercise stress testing).
  • Known Fontan baffle obstruction, branch pulmonary artery stenosis, or pulmonary vein stenosis resulting in a mean gradient of \>4 mmHg between the regions proximal and distal to the obstruction.
  • Single lung physiology.
  • Severe ventricular dysfunction or valvular regurgitation (systemic atrioventricular or semilunar valve) determined from review of the echocardiogram performed in closest proximity to study enrollment.
  • Significant renal (serum creatinine \> 2.0), hepatic (serum aspartate aminotransferase (AST) and/or alanine aminotransferase ( ALT) \> 3 times upper limit of normal), gastrointestinal or biliary disorders that could impair absorption, metabolism or excretion of orally administered medications, based on laboratory assessment at the time of screening visit.
  • Hospitalization for acute decompensated heart failure within the 12 months preceding study enrollment.
  • A diagnosis of active protein losing enteropathy or plastic bronchitis.
  • Active evaluation or listing for heart transplant.
  • History of use of a phosphodiesterase type 5 inhibitor within three months of study enrollment.
  • Concurrent illness that, in the opinion of the investigator, precludes participation.
  • Current therapy with alpha-blockers or nitrates.
  • Pregnancy at the time of enrollment.
  • Latex allergy

Key Trial Info

Start Date :

July 1 2014

Trial Type :

INTERVENTIONAL

Allocation :

ACTUAL

End Date :

April 1 2015

Estimated Enrollment :

36 Patients enrolled

Trial Details

Trial ID

NCT02201342

Start Date

July 1 2014

End Date

April 1 2015

Last Update

May 6 2025

Active Locations (6)

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Page 1 of 2 (6 locations)

1

Riley Hospital for Children

Indianapolis, Indiana, United States, 46201

2

University of Michigan Congenital Heart Center

Ann Arbor, Michigan, United States, 48109-4204

3

Cincinnati Children's Hospital Medical Center

Cincinnati, Ohio, United States, 45229

4

Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, United States, 19104