Status:

COMPLETED

Study of Dexpramipexole Chronic Sinusitis With Nasal Polyps and Eosinophilia

Lead Sponsor:

Knopp Biosciences

Conditions:

Chronic Sinusitis With Nasal Polyps and Eosinophilia

Eligibility:

All Genders

18-70 years

Phase:

PHASE2

Brief Summary

Phase 2, open-label, multi-center study to evaluate the clinical effects of oral administration of dexpramipexole for 6 months in subjects with chronic sinusitis with nasal polyps and eosinophilia.

Detailed Description

This open-labelled study will evaluate the safety and preliminary efficacy of dexpramipexole for reducing the number of eosinophils in the peripheral blood and in improving nasal polyp score when admi...

Eligibility Criteria

Inclusion

  • Male or female \>18 or \<70 years of age
  • Willing to practice effective contraception during the study and be willing and able to continue contraception for 1 month (females) or 3 months (males) after the last dose of study treatment
  • Confirmed diagnosis of chronic sinusitis with nasal polyps
  • Documented history of nasal eosinophilia
  • Documented peripheral absolute eosinophil count \>300 cells/μL
  • Bilateral total polyp score of \>4
  • Sino-nasal outcome test (SNOT-22) score of \>7
  • Using an intranasal corticosteroid spray or irrigation (\< 1000 μg/day beclomethasone or equivalent)

Exclusion

  • Acute sinusitis, concurrent nasal infection, or subjects who have had a nasal or upper respiratory tract infection within 2 weeks prior to baseline
  • CT scan suggestive of allergic fungal rhinosinusitis
  • Nasal septal deviation that would occlude at least one nostril
  • Nasal surgery (including polypectomy) within 6 months prior to baseline
  • History of more than 5 sinonasal surgeries requiring general anesthesia
  • History of more than 2 sinonasal surgeries that changed the lateral wall of the nose
  • History of cystic fibrosis, primary ciliary's dysfunction or Kartagener's syndrome
  • History of diagnosis with a parasitic infection
  • Hospitalization or emergency treatment for the treatment of asthma two or more times in the 12 months prior to baseline
  • Hospitalization for an acute asthmatic attack within 4 weeks prior to baseline
  • Forced expiratory volume (FEV1) of \<60% of predicted normal range
  • Treatment with a systemic corticosteroid or intra-polyp corticosteroid within 8 weeks prior to baseline or anticipated need for systemic corticosteroids during the study treatment period
  • Utilization of rescue oral corticosteroids for asthma or chronic sinusitis exacerbation more than one time within the past 1 year
  • Treatment with an investigational drug in the previous 30 days or 5-half-lives, whichever is longer
  • Treatment with a monoclonal antibody therapy including omalizumab (Xolair®), within 5-half-lives
  • Treatment with zileuton (Zyflo®) within 4 weeks of baseline
  • Treatment with pramipexole (Mirapex®) within 4 weeks of baseline
  • History of malignancy, including solid tumors and hematologic malignancies (except basal cell and squamous cell cancers of the skin that have been completely excised and cured)
  • History of human immunodeficiency virus (HIV) or hepatitis B or C
  • History of unstable or severe cardiac, hepatic, or renal disease, or other medically significant illness
  • Medical or other condition likely to interfere with subject's ability to undergo study procedures, adhere to visit schedule or comply with study requirements
  • Absolute neutrophil count \<2000 cells/μL at screening, or any documented history of neutropenia
  • Total IgE \>1500 IU/ml at any visit prior to baseline
  • Renal dysfunction, defined as an estimated glomerular filtration rate (eGFR) of ≤80 mg/dL at screening (estimation of creatinine clearance using the MDRD formula)
  • History of long QT syndrome or arrhythmia
  • Prolongation of QT/QTc interval (e.g., repeated demonstration of a QT/QTc interval \>450 ms) at screening or pre-dose on day 1
  • Clinically important abnormalities in resting ECG that may interfere with the interpretation of QTc interval changes at screening or pre-dose on day 1, including any of the following:
  • PR interval \>210 ms;
  • QRS \>110 ms;
  • Heart rate \<45 bpm or \>100 bpm (average of 3 assessments).
  • Pregnant women or women breastfeeding

Key Trial Info

Start Date :

August 1 2014

Trial Type :

INTERVENTIONAL

Allocation :

ACTUAL

End Date :

January 20 2017

Estimated Enrollment :

20 Patients enrolled

Trial Details

Trial ID

NCT02217332

Start Date

August 1 2014

End Date

January 20 2017

Last Update

May 18 2021

Active Locations (7)

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Page 1 of 2 (7 locations)

1

ENT Associates of South Florida

Boca Raton, Florida, United States, 33487

2

Johns Hopkins University

Baltimore, Maryland, United States, 21205

3

Brigham and Women's Hospital

Boston, Massachusetts, United States, 02115

4

Wake Research Associates

Raleigh, North Carolina, United States, 27612