Status:

COMPLETED

TRAMmoniTTR Study Genetic Screening of an At-risk Population for hATTR and Monitoring of TTR Positive Subjects

Lead Sponsor:

CENTOGENE GmbH Rostock

Collaborating Sponsors:

Alnylam Pharmaceuticals

Conditions:

Transthyretin Amyloidosis

Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy

Eligibility:

All Genders

18+ years

Brief Summary

National, multicenter, epidemiological, longitudinal protocol to investigate the hATTR prevalence in an at-risk population for Hereditary Transthyretin Amyloidosis (hATTR) and subjects diagnosed with ...

Detailed Description

Hereditary TransThyRetin Amyloidosis (hATTR) is a slowly progressive condition, that is transmitted as an autosomal dominant trait and is characterized by abnormal extracellular deposits of fibrillar,...

Eligibility Criteria

Inclusion

  • Inclusion Criteria:
  • Informed consent is obtained from the participant
  • The participant is 18 years of age or older
  • The participant has no diagnosis of alcoholism according to international guidelines
  • The participant has not undergone chemotherapy for any carcinoma
  • AND
  • The participant is at risk for hATTR due to two or more the factors listed below:
  • cardiomyopathy or polyneuropathy with no obvious etiology atypical Chronic Inflammatory Demyelinating Polyneuropathy (CIDP) or Motor Neuron Disease (MND)
  • autonomic dysfunction
  • hypertrophic cardiomyopathy or heart failure with preserved ejection fraction Left Ventricular Hypertrophy (LVH)
  • bilateral carpal tunnel syndrome
  • spinal stenosis or spinal radiculopathy
  • gait disorders
  • ocular changes involving vitreous opacities
  • unexplained weight loss \>5kg
  • renal abnormalities
  • family history of hATTR
  • based on imaging or biopsy suspected for the wild type TTR (ATTR) and not genetically tested for hATTR
  • OR • The participant is diagnosed with hATTR
  • OR
  • • The participant is a 1st or 2nd degree relative of the TTR positive subject
  • Exclusion Criteria
  • Informed consent is not obtained from the participant
  • The participant is younger than 18 years of age
  • The participant has a diagnosis of alcoholism according to International guidelines
  • The participant has undergone chemotherapy for any carcinoma
  • The participant is not at risk for hATTR

Exclusion

    Key Trial Info

    Start Date :

    July 20 2017

    Trial Type :

    OBSERVATIONAL

    Allocation :

    ACTUAL

    End Date :

    May 16 2025

    Estimated Enrollment :

    5028 Patients enrolled

    Trial Details

    Trial ID

    NCT03237494

    Start Date

    July 20 2017

    End Date

    May 16 2025

    Last Update

    June 29 2025

    Active Locations (84)

    Enter a location and click search to find clinical trials sorted by distance.

    Page 1 of 21 (84 locations)

    1

    Kepler Universitätsklinikum, Klinik für Interne 1 - Kardiologie und internistische Intensivmedizin; Cardiology

    Linz, Austria, 4021

    2

    Kepler Universitätsklinikum, Neuromed Campus; Neurology

    Linz, Austria, 4021

    3

    Universitätsklinikum Aachen, Neurology

    Aachen, Germany, 52074

    4

    Klinikum Westmünsterland GmbH, I. Medizinische Klinik und Interventionelle Kardiologie

    Ahaus, Germany, 48683