Status:

UNKNOWN

MB-CART19.1 in Patients With R/R ALL

Lead Sponsor:

Shanghai Children's Medical Center

Collaborating Sponsors:

Miltenyi Biomedicine GmbH

Conditions:

Precursor B-Lymphoblastic Lymphoma/Leukaemia Refractory

Eligibility:

All Genders

2-18 years

Phase:

PHASE2

Brief Summary

Precursor-B acute lymphoblastic leukemia (ALL) is the most common cancer in childhood. Despite major advances in ALL therapy, 20% of children and 40-50% of adults fail state-of-the art first-line trea...

Detailed Description

This is an open-label, non-randomized phase II paediatric study. In this study, eligible patients will receive autologous T cells transduced with the lentiviral vector pLTG1563 (MB-CART19.1) at a does...

Eligibility Criteria

Inclusion

  • Age ≤18 years (if deemed fit by treating investigator)
  • CD19 expression must be detected on the malignant cells by flow cytometry.
  • Patients with relapsed disease with \>5% blasts in BM (M2 or M3) after at least one standard chemotherapy and one salvage regimen who are ineligible for allogeneic stem cell transplant (alloSCT)
  • Patients have refractory disease activity precluding alloSCT at this time, or patients who have relapsed post alloSCT at least 100 days post-transplant, with no evidence of active GVHD, and no longer taking immunosuppressive agents for at least 30 days prior to enrollment.
  • Patients with combined extramedullary ALL are eligible if extramedullary disease has been successfully cleared by conventional therapy at the time of inclusion (e.g. intrathecal chemotherapy, orchiectomy). This includes patients with combined CNS-2 (\<5 WBC/µl CSF, with blasts on cytospin) or CNS-3 (5WBC/µl CSF, with blasts on cytospin) disease and patients with combined testicular relapse.
  • Patients and/or parents must give their written informed consent/assent.

Exclusion

  • Rapidly progressive disease that in the estimation of live less than 12 weeks
  • Isolated extramedullary relapse (CNS and/or testicular) in ALL
  • Current autoimmune disease, or history of autoimmune disease with potential CNS involvement
  • Active clinically significant CNS dysfunction (including but not limited to uncontrolled seizure disorders, cerebrovascular ischemia or hemorrhage, dementia, paralysis)
  • History of an additional malignancy other than non-melanoma skin cancer or carcinoma in situ unless disease free for ≥3 years.
  • Pulmonary function: Patients with pre-existing severe lung disease (FEV1 or FVC \< 65%) or an oxygen requirement of \>28% O2 supplementation or active pulmonary infiltrates on chest X-ray at the time scheduled for T cell infusion
  • Cardiac function: Fractional shortening \<28% or left ventricular ejection fraction \<50% by echocardiography
  • Renal function: Creatinine clearance \<50 mL/min/1.73 m2

Key Trial Info

Start Date :

December 1 2017

Trial Type :

INTERVENTIONAL

Allocation :

ESTIMATED

End Date :

December 31 2019

Estimated Enrollment :

10 Patients enrolled

Trial Details

Trial ID

NCT03321123

Start Date

December 1 2017

End Date

December 31 2019

Last Update

October 25 2017

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