Status:

COMPLETED

A Study of RG-012 in Subjects With Alport Syndrome

Lead Sponsor:

Genzyme, a Sanofi Company

Conditions:

Alport Syndrome

Eligibility:

All Genders

18-65 years

Phase:

PHASE1

Brief Summary

This is a Phase 1, open-label, multi-center study of the safety, pharmacodynamics, and pharmacokinetics of RG-012 administered to subjects with Alport syndrome.

Detailed Description

This is a Phase 1, multi-center study of the safety, pharmacodynamics, and pharmacokinetics of RG-012 administered to subjects with Alport syndrome. During this open-label study, all eligible subjects...

Eligibility Criteria

Inclusion

  • Males or females, ages 18 to 65 years
  • Confirmed diagnosis of Alport syndrome
  • eGFR between 40 and 90 mL/min/1.73m2
  • Proteinuria of at least 300 mg protein/g creatinine
  • For subjects taking an ACE inhibitor or an ARB, the dosing regimen should be stable for at least 30 days prior to screening
  • Willing to comply with contraception requirements

Exclusion

  • Causes of chronic kidney disease aside from Alport syndrome (such as diabetic nephropathy, hypertensive nephropathy, lupus nephritis, or IgA nephropathy)
  • End stage renal disease (ESRD) as evidenced by ongoing dialysis therapy or history of renal transportation
  • Any other condition that may pose a risk to the subject's safety and well-being
  • Female subjects who are pregnant or lactating

Key Trial Info

Start Date :

December 22 2017

Trial Type :

INTERVENTIONAL

Allocation :

ACTUAL

End Date :

May 20 2019

Estimated Enrollment :

4 Patients enrolled

Trial Details

Trial ID

NCT03373786

Start Date

December 22 2017

End Date

May 20 2019

Last Update

April 25 2022

Active Locations (7)

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Page 1 of 2 (7 locations)

1

eStudySite

La Mesa, California, United States, 91942

2

Academic Medical Research Institute

Los Angeles, California, United States, 90022

3

Apex Research of Riverside

Riverside, California, United States, 92505

4

Eminence Medical & Clinical Research

Tampa, Florida, United States, 33604