Status:

COMPLETED

Nutrition Status of Adults Treated With Pegvaliase

Lead Sponsor:

Boston Children's Hospital

Collaborating Sponsors:

BioMarin Pharmaceutical

Conditions:

Phenylketonurias

Eligibility:

All Genders

18-65 years

Brief Summary

Conduct a cross-sectional analysis of the nutritional status of individuals with PKU treated with pegvaliase for one or more years or who have followed an unrestricted diet for 6 or more months while ...

Eligibility Criteria

Inclusion

  • Diagnosis of phenylketonuria
  • Aged 18-65 years
  • Currently treated with pegvaliase
  • Have either 1) received treatment with pegvaliase for one or more years or 2) followed an unrestricted diet for 6 or more months while on pegvaliase
  • Currently following an unrestricted diet that meets or exceeds the RDA for protein (0.8 g/kg/day)

Exclusion

  • Unable to consent to study
  • Under age 18 years or over age 65
  • Routine food intake provides less than the RDA for protein (0.8 g/kg/d)
  • Consuming any PKU medical foods

Key Trial Info

Start Date :

January 17 2019

Trial Type :

OBSERVATIONAL

Allocation :

ACTUAL

End Date :

December 31 2020

Estimated Enrollment :

18 Patients enrolled

Trial Details

Trial ID

NCT03792451

Start Date

January 17 2019

End Date

December 31 2020

Last Update

March 4 2021

Active Locations (1)

Enter a location and click search to find clinical trials sorted by distance.

Page 1 of 1 (1 locations)

1

Boston Children's Hospital

Boston, Massachusetts, United States, 02115