Status:

COMPLETED

A Study to Evaluate Isavuconazonium Sulfate for the Treatment of Invasive Aspergillosis (IA) or Invasive Mucormycosis (IM) in Pediatric Participants

Lead Sponsor:

Astellas Pharma Global Development, Inc.

Conditions:

Invasive Mucormycosis

Invasive Aspergillosis

Eligibility:

All Genders

1-17 years

Phase:

PHASE2

Brief Summary

The purpose of this study was to evaluate the safety, tolerability, and efficacy of isavuconazonium sulfate in pediatric participants.

Detailed Description

Treatment began on Day 1 and then participants were followed for 60 days post-last dose for safety. Treatment was administered until the participant had a successful outcome or for a maximum duration ...

Eligibility Criteria

Inclusion

  • Subject diagnosed with IA or IM. A positive diagnosis is defined as follows:
  • Proven, probable or possible IFI per the European Organisation for Research and Treatment of Cancer/Mycoses Study Group \[EORTC/MSG\], 2008 criteria Note: Subjects with "possible" IFI will be eligible for enrollment; however, diagnostic tests to confirm the invasive fungal disease as "probable" or "proven" according to the EORTC/MSG criteria should be completed within 10 calendar days after the first dose of study drug
  • Note: In addition to the criteria set for mycological criteria by the EORTC/MSG in 2008, and only for subjects with an underlying hematologic malignancy or recipients of hematopoietic stem cell transplant (HSCT) who also have clinical and radiologic features consistent with invasive fungal infection, the following are acceptable:
  • Galactomannan (GM) levels (optical density index) meeting the below criteria are acceptable mycological evidence for enrollment or upgrading the diagnosis to probable IA:
  • 1\. A single value for serum or bronchoalveolar lavage (BAL) fluid of ≥ 1.0 or
  • 2\. Two serum GM values of ≥ 0.5 from two separate samples
  • Subject has sufficient venous access to permit intravenous administration of study drug or the ability to swallow oral capsules
  • A female subject is eligible to participate if not pregnant and at least one of the following conditions applies:
  • Not a subject who is of childbearing potential, OR
  • Subject who is of childbearing potential who agrees to follow a contraceptive guidance throughout the treatment period and for at least 30 days after the final study drug administration
  • Subject and subject's parent(s) or legal guardian agree that the subject will not participate in another interventional study while on treatment with the exception of oncology trials

Exclusion

  • Subject has familial short QT syndrome, is receiving medications that are known to shorten the QT interval, or has a clinically significant abnormal ECG
  • Subject has evidence of hepatic dysfunction defined as any of the following:
  • Total bilirubin (TBL) ≥ 3 times the upper limit of normal (ULN)
  • Alanine transaminase (ALT) or aspartate transaminase (AST) ≥ 5 times the ULN
  • Known cirrhosis or chronic hepatic failure
  • Subject has used strong cytochrome P450 (CYP3A4) inhibitors or inducers such as ketoconazole, high dose ritonavir, rifampin/rifampicin, long acting barbiturates (e.g., phenytoin), carbamazepine and St. John's Wort in the 5 days prior to the first dose of study drug
  • Subject has another IFI other than possible, probably or proven IA or IM
  • Subject has chronic aspergillosis, aspergilloma or allergic bronchopulmonary aspergillosis
  • Subject has received mould active systemic antifungal therapy, effective against the primary IMI, for more than four days during the seven days preceding the first dose
  • Note: Prior use of prophylactic antifungal therapy is acceptable. In case of breakthrough IA while on prophylactic mould-active azole class drugs, additional documentation will be required to be submitted to the sponsor medical monitor or designee to approve subject enrollment
  • Subject has known history of allergy, hypersensitivity or any serious reaction to any of the azole class antifungals, or any components of the study drug formulation
  • Subject has any condition which makes the subject unsuitable for study participation
  • Subject is unlikely to survive 30 days
  • Subject has received investigational drug, with the exception of oncology drug trials, or trials with investigational drugs treating graft versus host disease, within 28 days or five half-lives, whichever is longer, prior to screening

Key Trial Info

Start Date :

August 22 2019

Trial Type :

INTERVENTIONAL

Allocation :

ACTUAL

End Date :

December 14 2022

Estimated Enrollment :

31 Patients enrolled

Trial Details

Trial ID

NCT03816176

Start Date

August 22 2019

End Date

December 14 2022

Last Update

December 5 2024

Active Locations (10)

Enter a location and click search to find clinical trials sorted by distance.

Page 1 of 3 (10 locations)

1

Children's Hospital, Los Angeles

Los Angeles, California, United States, 90027

2

University of California - Los Angeles

Los Angeles, California, United States, 90095

3

Children's Hospital of Orange County

Orange, California, United States, 92868

4

Children's National Medical Center

Washington D.C., District of Columbia, United States, 20010