Status:

COMPLETED

A Study to Assess the Safety, Tolerability, and Pharmacokinetics of Single and Multiple Doses of Cefiderocol in Hospitalized Pediatric Participants

Lead Sponsor:

Shionogi

Conditions:

Gram-negative Bacterial Infections

Bloodstream Infections (BSI)

Eligibility:

All Genders

3-17 years

Phase:

PHASE2

Brief Summary

The primary objectives of this study are: * To assess the safety and tolerability of cefiderocol after single-dose administration in hospitalized paediatric participants 3 months to \< 18 years of ag...

Detailed Description

This is a multicenter, single-arm, open-label, single- and multiple-dose study to assess the safety, tolerability, and PK of cefiderocol in hospitalized paediatric participants. The single-dose phase...

Eligibility Criteria

Inclusion

  • Participant's parent(s) or legally authorized representative (LAR) provides written informed consent in accordance with regional and country-specific laws and regulations.
  • Participant provides written informed assent, when feasible (age of assent to be determined by institutional review boards/independent ethics committees \[IRB's/IEC's\] or be consistent with local legal requirements).
  • Hospitalized participant is 3 months to \<18 years of age at the time written informed consent/assent is obtained for the single-dose phase. Hospitalized participant is 3 months to \<12 years of age at the time written informed consent/assent is obtained for the multiple-dose phase. Premature babies will not be restricted, but the participant must have an adjusted or postnatal age of 3 months.
  • Participant has a suspected or confirmed infection (including but not limited to complicated urinary tract infection \[cUTI\], complicated intra-abdominal infection \[cIAI\], hospital-acquired pneumonia \[HAP\] /ventilator-acquired pneumonia \[VAP\], sepsis, or bloodstream infections \[BSI\]) that requires hospitalization for treatment with IV antibiotics.
  • If participant is a sexually active female of childbearing potential and has reached menarche or Tanner stage 3, participant agrees to use barrier contraception (including condom, diaphragm, or cervical cap) with spermicide or agrees to use a highly effective method of contraception (including contraceptive implant, injectable contraceptive, combination oral contraceptive, or an intrauterine \[IUD\] contraceptive device) from Screening up to 28 days after administration of the last dose of cefiderocol.

Exclusion

  • Participant has a documented history of any hypersensitivity or allergic reaction to any β-lactam antibiotic (Note: for β-lactams, a history of a mild rash followed by uneventful re-exposure is not a contraindication to enrollment).
  • Multiple-dose only: Participant has an infection caused only by a confirmed Gram-positive pathogen.
  • Participant has a suspected or confirmed central nervous system (CNS) infection (eg, meningitis, brain abscess, shunt infection) or osteomyelitis (which would require prolonged antibiotic therapy).
  • Participant has cystic fibrosis.
  • Single-dose phase: Participant has moderate or severe renal impairment based on estimated glomerular filtration rate (eGFR) (based on Schwartz equation if ≥ 3 months to \< 1 year of age and modified Bedside Schwartz equation if ≥ 1 to \< 18 years of age) of \< 60 milliliter (mL) per minute (min)/1.73 \^2² at Screening.
  • Multiple-dose phase: Participant has an eGFR (based on Schwartz equation if ≥ 3 months to \< 1 year of age and modified Bedside Schwartz equation if ≥ 1 to \< 18 years of age) of \< 15 mL/min/1.73 \^2² at Screening.
  • Participant has end-stage renal disease (ESRD), is on hemodialysis (HD), or receiving continuous venovenous hemofiltration (CVVH).
  • Participant has experienced shock in the prior month or is in shock at the time of Screening.
  • Participant has severe neutropenia or is severely immunocompromised.
  • Participant has multiorgan failure.
  • Participant has a life expectancy of \< 30 days due to severity of a concurrent illness.
  • Participant is a female who has a positive pregnancy test at Screening.
  • Participant is a female who is breastfeeding.
  • Participant has received any other investigational medicinal product (IMP) within 30 days.
  • Participant has any condition or circumstance that, in the opinion of the investigator, would compromise the safety of the participant or the quality of the study data, including acute trauma to the pelvis or urinary tract.
  • Participant is receiving vasopressor therapy at Screening.

Key Trial Info

Start Date :

August 21 2020

Trial Type :

INTERVENTIONAL

Allocation :

ACTUAL

End Date :

February 6 2023

Estimated Enrollment :

54 Patients enrolled

Trial Details

Trial ID

NCT04335539

Start Date

August 21 2020

End Date

February 6 2023

Last Update

January 24 2024

Active Locations (23)

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Page 1 of 6 (23 locations)

1

Universitair Ziekenhuis Brussel

Brussels, Belgium, 1200

2

Cliniques Universitaires Saint-Luc

Brussels, Belgium

3

Tallinn Childrens Hospital

Tallinn, Estonia

4

Tartu Ulikooli Kliinikum - Anestesioloogia ja Intensiivravi Kliinik

Tartu, Estonia