Status:

ACTIVE_NOT_RECRUITING

Identification and Characterization of Novel Non-Coding Variants That Contribute to Genetic Disorders

Lead Sponsor:

Duke University

Conditions:

Genetic Disease

Inborn Errors of Metabolism

Eligibility:

All Genders

Brief Summary

The goal of this study is to identify and characterize novel non-coding and splicing variants that may contribute to genetic disorders. We will particularly focus on patients with a diagnosed genetic ...

Detailed Description

To perform this study, we will use patient DNA and RNA that is isolated from blood samples. DNA will be sequenced (targeted capture and/or whole genome DNA sequencing (WGS)) to identify any non-coding...

Eligibility Criteria

Inclusion

  • Inclusion criteria:
  • Subjects will have one or more of the following:
  • Patients (probands) diagnosed with a genetic disease
  • Patients (probands) with inconclusive genetic results
  • Patients (probands) that have identical coding and/or splicing variants, but display highly diverse phenotypes
  • Unaffected family members of probands
  • Exclusion Criteria: There are no exclusion criteria for this study.

Exclusion

    Key Trial Info

    Start Date :

    March 3 2020

    Trial Type :

    OBSERVATIONAL

    Allocation :

    ACTUAL

    End Date :

    September 1 2027

    Estimated Enrollment :

    56 Patients enrolled

    Trial Details

    Trial ID

    NCT04399694

    Start Date

    March 3 2020

    End Date

    September 1 2027

    Last Update

    October 15 2025

    Active Locations (1)

    Enter a location and click search to find clinical trials sorted by distance.

    Page 1 of 1 (1 locations)

    1

    Duke University

    Durham, North Carolina, United States, 27710