Status:

TERMINATED

Tranexamic Acid Use to Reduce Blood Transfusion in Pediatric Cancer Patients Undergoing Limb Salvage Procedure

Lead Sponsor:

St. Jude Children's Research Hospital

Conditions:

Cancer of the Bone

Limb Salvage

Eligibility:

All Genders

Up to 24 years

Phase:

PHASE3

Brief Summary

This is a randomized double-blind control trial evaluating the use Tranexamic acid (TXA) to decrease blood loss and transfusion requirements in pediatric and young adult cancer patients undergoing a l...

Detailed Description

Eligible participants undergoing limb salvage procedures will be randomized to receive either tranexamic acid (TXA) or placebo peri-operatively. The initial dose of tranexamic acid/placebo will be gi...

Eligibility Criteria

Inclusion

  • Participant undergoing limb salvage procedure of malignant bone tumor of the distal femur or proximal tibia, which typically requires blood transfusions.
  • Patient under the age of 25
  • Adequate bone marrow function defined as:
  • Upward trending peripheral absolute neutrophil count (ANC)
  • Platelet count ≥ 100,000/mm\^3 (transfusion independent defined as no platelets required for 4 days)
  • Hemoglobin ≥ 8.0 g/dL
  • No RBC transfusion within 24 hours
  • Adequate renal function defined as:
  • Creatinine clearance or radioisotope GFR ≥ 70 mL/min/1.73m\^2 OR
  • Maximum serum creatinine based on age/gender as follows: Age 1 day to \< 1 years: maximum serum creatinine (mg/dL) 0.6 for males and 0.5 for females; Age 1 to \< 2 years: maximum serum creatinine (mg/dL) 0.6 for males and 0.6 for females; Age 2 to \< 6 years: maximum serum creatinine (mg/dL) 0.8 for males and 0.8 for females; Age 6 to \< 10 years: maximum serum creatinine (mg/dL) 1.0 for males and 1.0 for females; Age 10 to \< 13 years: maximum serum creatinine (mg/dL) 1.2 for males and 1.2 for females; Age 13 to \< 16 years: maximum serum creatinine (mg/dL) 1.5 for males and 1.4 for females; Age ≥ 16 years: maximum serum creatinine (mg/dL) 1.7 for males and 1.4 for females
  • Adequate liver function defined as:
  • Total bilirubin ≤ 1.5x the institutional upper limit of normal (IULN) for age
  • ALT (SGPT) and AST (SGOT) ≤ 2.5x IULN for age (or \<5x IULN for patients with documented disease involving the liver or 10x IULN for patients receiving HDMTX)
  • Serum albumin \> 2 g/dL
  • Adequate coagulation function as defined by International Normalized Ratio (INR) ≤ 1.5
  • Female participants of child-bearing potential (\>10 years old) must have a negative serum or urine pregnancy test within 72 hours of sedation

Exclusion

  • Participants whose limb salvage procedure may require significant manipulation of major blood vessels.
  • Participants with known bone marrow deficiency resulting in red blood cell deficiency (e.g. Diamond-Blackfan anemia)
  • Participants receiving erythropoietin-stimulating agents (e.g. epoetin alfa)
  • Participants with active hemorrhagic cystitis (e.g. alkylator-induced) with gross hematuria or \>50 RBCs per high powered field on urinalysis
  • Participants actively receiving all-trans retinoic acid (ATRA) or isotretinoin (Accutane)
  • Participants with known allergies to antifibrinolytics
  • Participants with known hypercoagulopathies
  • Personal history of a thrombosis or active thrombus
  • Participants currently on anticoagulation medications (e.g. warfarin, enoxaparin)
  • Participants with a history of seizures. Patients with a history of febrile seizure are eligible.
  • Persisting toxicity related to other systemic therapies (e.g. chemotherapy) which constitutes an unacceptable safety risk based on the judgment of the PI and/or the primary treating physician.
  • Female participants who are currently pregnant or actively breastfeeding.
  • Female participants who are currently receiving estrogen-based contraception therapy.
  • Inability or unwillingness of research participant or legal guardian/representative to give written informed consent.
  • Participants enrolled in another clinical trial utilizing an IND/IDE experimental therapy.
  • Participants with a history of CNS disease.
  • Participants with known bleeding disorder.
  • Participants with known platelet dysfunction.

Key Trial Info

Start Date :

January 29 2021

Trial Type :

INTERVENTIONAL

Allocation :

ACTUAL

End Date :

January 16 2024

Estimated Enrollment :

15 Patients enrolled

Trial Details

Trial ID

NCT04410042

Start Date

January 29 2021

End Date

January 16 2024

Last Update

December 20 2024

Active Locations (1)

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St. Jude Children's Research Hospital

Memphis, Tennessee, United States, 38105