Status:

RECRUITING

A Phase 1/2, Open-label, Safety and Dosing Study of Autologous CART Cells (Desmoglein 3 Chimeric Autoantibody Receptor T Cells [DSG3-CAART] or CD19-specific Chimeric Antigen Receptor T Cells [CABA-201]) in Subjects With Active, Pemphigus Vulgaris (RESET-PV)

Lead Sponsor:

Cabaletta Bio

Conditions:

Pemphigus Vulgaris

Eligibility:

All Genders

18+ years

Phase:

PHASE1

PHASE2

Brief Summary

A phase 1/2, open-label, safety and dosing study of autologous CART cells (desmoglein 3 chimeric autoantibody receptor T cells \[DSG3-CAART\] or CD19-specific Chimeric Antigen Receptor T cells \[CABA-...

Detailed Description

Pemphigus vulgaris (PV) is a B-cell mediated autoimmune disorder in which painful blisters are formed on the skin or mucosal membrane, including the mouth, nose, throat, eyelids, anus, and genitals. ...

Eligibility Criteria

Inclusion

  • Inclusion Criteria for DSG3-CAART: Closed to enrollment
  • Confirmed diagnosis of mPV by prior or screening biopsy and prior positive anti- DSG3 antibody ELISA
  • mPV inadequately managed by at least one standard immunosuppressive therapies
  • Active mPV at screening
  • Anti-DSG3 antibody ELISA positive at screening
  • Inclusion Criteria for CABA-201 sub-study: Open to enrollment
  • Age ≥18
  • Confirmed diagnosis of PV by prior or screening biopsy and prior positive DSG3 ELISA, IIF, and/or DIF
  • PV inadequately managed by at least one standard immunosuppressive therapy
  • Active PV at screening
  • DSG3 ELISA positive at screening
  • Exclusion Criteria:
  • Active cutaneous lesions associated with PV that indicates mucocutaneous rather than mucosal-dominant disease
  • Rituximab in last 12 months unless PV symptoms have recently worsened or anti-DSG3 antibody titers have recently increased
  • Prednisone \> 0.25mg/kg/day
  • Other autoimmune disorder requiring immunosuppressive therapies
  • Investigational treatment in last 3 months
  • Exclusion Criteria for CABA-201 sub-study
  • Have paraneoplastic pemphigus or active malignancy (not including non-melanoma skin cancer) or malignancy diagnosed within the previous 5 years
  • Have received rituximab or other anti-CD20 or anti-CD19 therapies in last 12 months unless anti-DSG3 antibody titers have recently increased or PV symptoms have recently worsened
  • Prednisone \> 0.25mg/kg/day
  • Other autoimmune disorder requiring immunosuppressive therapies
  • Treatment with any investigational agent within 4 weeks or 5 half-lives, whichever is longer.

Exclusion

    Key Trial Info

    Start Date :

    September 29 2020

    Trial Type :

    INTERVENTIONAL

    Allocation :

    ESTIMATED

    End Date :

    January 1 2029

    Estimated Enrollment :

    40 Patients enrolled

    Trial Details

    Trial ID

    NCT04422912

    Start Date

    September 29 2020

    End Date

    January 1 2029

    Last Update

    December 17 2025

    Active Locations (13)

    Enter a location and click search to find clinical trials sorted by distance.

    Page 1 of 4 (13 locations)

    1

    Stanford University, Dept. of Dermatology

    Redwood City, California, United States, 94063

    2

    UC Davis, Dept. of Dermatology

    Sacramento, California, United States, 95816

    3

    Yale University

    New Haven, Connecticut, United States, 06520

    4

    Northwestern University

    Chicago, Illinois, United States, 60611