Status:

COMPLETED

Sirolimus Treatment for Newly Diagnosed Primary Acquired PRCA

Lead Sponsor:

Bing Han

Conditions:

Pure Red Cell Aplasia, Acquired

Eligibility:

All Genders

18-88 years

Phase:

PHASE4

Brief Summary

Pure red cell aplasia (PRCA) is a kind of anemia characterized by severe reticulocytopenia and obvious bone marrow erythroblastic cells decreased. Cyclosporine A and /or steroids are the first line th...

Detailed Description

Pure red cell aplasia (PRCA) is a rare normocytic normochromic anemia with reticulocytopenia, characterized by a reduction of erythroid precursors from the bone marrow, could be divided into congenita...

Eligibility Criteria

Inclusion

  • age \>18 years old.
  • hemoglobin (Hb) \<90 g/L before treatment.
  • no history of immunosuppression therapy prior to sirolimus or CsA treatment.
  • adequate hepatic functions with alanine transaminase (ALT)/aspartate. transaminase (AST) levels within 3 times of the normal upper limit and total bilirubin levels within 2 times of the normal upper limit.
  • documented patient consent.

Exclusion

  • diagnosis of secondary aPRCA.
  • history of treatment with immunosuppression therapy before enrollment.
  • history of leukemia, stem cell transplantation, or treatment-related myelodysplastic syndromes (MDS).
  • creatinine/transaminase ≥ 3 normal upper limit.
  • complicated with active or uncontrolled infections or uncontrolled cardiovascular disease.
  • presence of other diseases that may cause anemia.
  • presence of malignancies.
  • pregnant and lactating women.

Key Trial Info

Start Date :

July 1 2020

Trial Type :

INTERVENTIONAL

Allocation :

ACTUAL

End Date :

July 31 2022

Estimated Enrollment :

56 Patients enrolled

Trial Details

Trial ID

NCT04470804

Start Date

July 1 2020

End Date

July 31 2022

Last Update

February 28 2023

Active Locations (1)

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Page 1 of 1 (1 locations)

1

Peking Union Medical College Hospital

Beijing, China, 100730