Status:

ACTIVE_NOT_RECRUITING

A Study to Evaluate the Efficacy, Drug Levels and Safety of Luspatercept (ACE-536) for the Treatment of Anemia Due to IPSS-R Very Low, Low, or Intermediate Risk Myelodysplastic Syndromes in Chinese and Japanese Participants With Ring Sideroblasts Who Require Red Blood Cell Transfusions

Lead Sponsor:

Celgene

Conditions:

Myelodysplastic Syndromes

Eligibility:

All Genders

20+ years

Phase:

PHASE2

Brief Summary

The purpose of this study is to evaluate the efficacy and safety of luspatercept (ACE-536) for the treatment of anemia due to Revised International Prognostic Scoring System (IPSS-R) very low, low, or...

Eligibility Criteria

Inclusion

  • Refractory or intolerant to, or ineligible for, prior Erythropoiesis stimulating agent (ESA) treatment as defined by any one of the following: Refractory to prior ESA treatment, Intolerant to prior ESA treatment, or ESA ineligible.
  • previously treated with an ESA or granulocyte colony-stimulating factor, granulocyte-macrophage colony-stimulating factor, both agents must have been discontinued ≥ 4 weeks prior to date of luspatercept treatment
  • Eastern Cooperative Oncology Group (ECOG) score of 0, 1, or 2

Exclusion

  • Prior therapy with disease modifying agents for underlying MDS disease
  • Known clinically significant anemia due to iron, vitamin B12, or folate deficiencies, or autoimmune or hereditary hemolytic anemia, or gastrointestinal bleeding
  • Serum aspartate aminotransferase/serum glutamic oxaloacetic transaminase (AST/SGOT) or alanine aminotransferase/serum glutamic pyruvic transaminase (ALT/SGPT) ≥ 3.0 x upper limit of normal (ULN)
  • Other protocol-defined inclusion/exclusion criteria apply

Key Trial Info

Start Date :

November 30 2020

Trial Type :

INTERVENTIONAL

Allocation :

ACTUAL

End Date :

February 23 2026

Estimated Enrollment :

30 Patients enrolled

Trial Details

Trial ID

NCT04477850

Start Date

November 30 2020

End Date

February 23 2026

Last Update

October 12 2023

Active Locations (24)

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Page 1 of 6 (24 locations)

1

Local Institution - 100

Beijing, China, 100730

2

Local Institution - 107

Chengdu, Sichuan, China, 610041

3

Local Institution - 105

Guangzhou, China, 510060

4

Local Institution - 103

Guangzhou, China, 510080