Status:

COMPLETED

Study of Oral Idebenone to Treat Non-Alcoholic Steatohepatitis

Lead Sponsor:

Stanford University

Collaborating Sponsors:

National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)

Conditions:

Non Alcoholic Steatohepatitis

Fibrosis

Eligibility:

All Genders

18+ years

Phase:

PHASE1

PHASE2

Brief Summary

This is a randomized, placebo-controlled phase 1/2a study to investigate the safety and tolerability of Idebenone in patients 18 years of age or older with non-alcoholic steatohepatitis, with stage 1-...

Detailed Description

This is a prospective phase 1/2a, randomized, double-blinded, placebo-controlled, single center study of safety and efficacy of oral idebenone in adults 18 years of age or older with non-alcoholic ste...

Eligibility Criteria

Inclusion

  • 1\) Male or non-pregnant/ non-lactating women ≥ 18 years of age
  • 2\) Diagnosis of NASH: NAFLD activity score (NAS) of 4 or greater with a score of 1 for each of the following (steatosis scored 0-3, lobular inflammation scored 0-3, ballooning scored 0-2):
  • Steatosis
  • Lobular inflammation
  • Hepatocyte ballooning 3) Fibrosis (Ishak fibrosis score ≥1 on liver biopsy) within 6 months of enrollment with MELD\<10, or based on MRE

Exclusion

  • Presence of any other form of liver disease, including viral hepatitis, autoimmune hepatitis, alcoholic liver disease, genetic causes of chronic liver disease):
  • Subjects with other etiologies of chronic liver disease, such as chronic hepatitis B and C; autoimmune hepatitis; and inherited liver disease.
  • ALT\>300 U/l
  • Total serum bilirubin ≥ to 1.3 mg/dL (Gilbert's Syndrome patients excepted)
  • International Normalized Ratio (INR) ≥ 1.3
  • MELD\>10
  • Serum creatinine \>2.0mg/dl
  • Known alcohol abuse or alcohol use disorder:
  • \>20 g/day for women
  • \>30 g/day for men
  • Active substance abuse
  • Any medical condition that prevents MRE, MR-PDFF
  • Platelet count ≤100//mm3
  • Decompensated cirrhosis
  • Hemoglobin \<11 g/dl in females or \<12 g/dl in males
  • Presence/history of HCC
  • History of liver transplantation
  • History of bariatric surgery
  • History of inflammatory bowel disease
  • History of cardiovascular disease, long QT syndrome.
  • Subjects who have participated in investigational drug trials and took any investigational drugs within 60 days prior to the first dose of Idebenone. History of receiving other investigations drug within 30 days prior to enrollment
  • Any concerns regarding compliance by enrolling physician

Key Trial Info

Start Date :

July 30 2021

Trial Type :

INTERVENTIONAL

Allocation :

ACTUAL

End Date :

July 5 2023

Estimated Enrollment :

45 Patients enrolled

Trial Details

Trial ID

NCT04669158

Start Date

July 30 2021

End Date

July 5 2023

Last Update

September 23 2025

Active Locations (2)

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Page 1 of 1 (2 locations)

1

Digestive Health Center, Stanford University

Redwood City, California, United States, 94063

2

Stanford University

Stanford, California, United States, 94305