Status:
ACTIVE_NOT_RECRUITING
Outcome Measures and Biomarkers in a Cohort of Spinal Muscular Atrophy Type III/ IV Patients
Lead Sponsor:
Assistance Publique Hopitaux De Marseille
Conditions:
Spinal Muscular Atrophy
Eligibility:
All Genders
18-70 years
Phase:
NA
Brief Summary
The "SMOB" project intends to contribute to fill the gap with reliable and operational outcome measures for type III and IV SMA. In analysing the reliability in imaging (spinal and muscular), electrop...
Detailed Description
Spinal muscular atrophy is an autosomal recessive neurodegenerative disease characterized by degeneration of spinal cord motor neurons, atrophy of skeletal muscles, and generalized weakness. It is cau...
Eligibility Criteria
Inclusion
- Men or women
- Between 18 and 70 years old
- Given written informed consent after being informed of the purpose, progress and potential risks
Exclusion
- Concomitant impairment of central nervous system (for example cervical myelopathy)
- Homeless patients
- Deprived of their liberty by a court or administrative order or under guardianship
- Unable to understand the purpose and conditions of carrying out the study, unable to give consent
- Patients included in another clinical trial or exclusion period from a previous clinical trial
Key Trial Info
Start Date :
July 13 2021
Trial Type :
INTERVENTIONAL
Allocation :
ACTUAL
End Date :
October 8 2025
Estimated Enrollment :
104 Patients enrolled
Trial Details
Trial ID
NCT04690998
Start Date
July 13 2021
End Date
October 8 2025
Last Update
August 6 2024
Active Locations (11)
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1
Service de Neurologie,Hôpital Raymond-Poincaré
Garches, France, 92380
2
Département de Neurologie - CHRU Lille
Lille, France, 59037
3
Service ENMG - Pathologies neuromusculaires, centre de référence en pathologie neuromusculaire Rhône-Alpes, Centre de référence SLA
Lyon, France, 69677
4
CHU Montpellier
Montpellier, France, 34090