Status:
RECRUITING
International Registry of Patients With Alpha Thalassemia
Lead Sponsor:
University of California, San Francisco
Conditions:
Alpha-Thalassemia
Alpha Thalassemia Major
Eligibility:
All Genders
Brief Summary
This is an international prospective registry of patients with Alpha thalassemia to understand the natural history of the disease and the outcomes of fetal therapies, with the overall goal of improvin...
Detailed Description
The aim of this registry is to prospectively and retrospectively collect data on patients who are diagnosed with alpha thalassemia major and other alpha thalassemia mutations. Data collected will be u...
Eligibility Criteria
Inclusion
- diagnosis of alpha thalassemia (prenatal or postnatal) with genotype consistent with ATM or BHFS phenotype
- referred to the University of California, San Francisco Fetal Treatment Center for fetal diagnosis, management and/or evaluation for the ongoing in utero stem cell transplantation clinical trial
Exclusion
- \- none
Key Trial Info
Start Date :
January 1 2017
Trial Type :
OBSERVATIONAL
Allocation :
ESTIMATED
End Date :
January 1 2037
Estimated Enrollment :
500 Patients enrolled
Trial Details
Trial ID
NCT04872179
Start Date
January 1 2017
End Date
January 1 2037
Last Update
April 4 2025
Active Locations (1)
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1
University of California San Francisco
San Francisco, California, United States, 94143