Status:

COMPLETED

A Study to Assess RXC004 Efficacy in Advanced Solid Tumours After Progression on Standard of Care (SoC) Therapy (PORCUPINE2)

Lead Sponsor:

Redx Pharma Ltd

Collaborating Sponsors:

Merck Sharp & Dohme LLC

Conditions:

Advanced Solid Tumours

Eligibility:

All Genders

18+ years

Phase:

PHASE2

Brief Summary

This study is to evaluate the preliminary efficacy and safety of RXC004 monotherapy and in combination with pembrolizumab in advanced solid tumours that have progressed following SoC treatment.

Detailed Description

This Phase II, modular, open label, multicentre study initially opened with ring finger protein 43 (RNF43) loss of function (LoF) mutation-positive pancreatic ductal adenocarcinoma (PDAC) (Module 1) a...

Eligibility Criteria

Inclusion

  • Core
  • At least one lesion that is measurable by RECIST 1.1 at baseline (within 6 weeks prior to start of study treatment).
  • Mandatory paired biopsies; Patients must have at least one lesion suitable for biopsy at screening
  • Adequate organ and marrow function
  • Female patients of childbearing potential must have a negative pregnancy test prior to start of dosing
  • Female patients of childbearing potential and male patients with female partners of childbearing potential must agree to use a highly effective method of contraception during the study from the time of treatment initiation, and for at least 5 months after the last dose of study drug.
  • Module 1 (PDAC) Specific Inclusion Criteria
  • Histological documentation of advanced (unresectable)/metastatic (Stage III/IV) PDAC, with documented loss of function tumour mutation in RNF43
  • Patients must have received one prior systemic treatment for advanced (unresectable)/metastatic PDAC (Stage III/IV), with clear evidence of radiological disease progression
  • Patients must be enrolled and receive first dose of study treatment within 6 weeks of radiologically confirmed progression
  • Karnofsky performance status ≥70.
  • Module 2 and Module 3 (BTC) Specific Inclusion Criteria
  • Histological documentation of advanced (unresectable)/metastatic (Stage III/IV) BTC (intrahepatic or extrahepatic cholangiocarcinoma, ampulla of Vater, or gallbladder cancer)
  • Patients must have received one prior systemic treatment for advanced (unresectable)/metastatic BTC, with clear evidence of radiological disease progression
  • Patients must be enrolled and receive first dose of study treatment within 6 weeks of radiologically confirmed progression
  • ECOG status 0 or 1.
  • Core

Exclusion

  • Prior therapy with a compound of the same mechanism of action as RXC004
  • Patients at higher risk of bone fractures
  • Any known uncontrolled inter-current illness or persistent clinically significant toxicity related to prior anti-cancer treatment
  • Patients who have any history of an active (requiring treatment) other malignancy within 2 years of study entry
  • Patients with known or suspected brain metastases
  • Use of anti-neoplastic agents
  • Patients with a known hypersensitivity to any RXC004 excipients
  • Patients with a contra-indication for denosumab treatment
  • Patients who are pregnant or breast-feeding
  • Known active human immunodeficiency viruses (HIV), hepatitis B (HBV), or hepatitis C (HCV) infections
  • Use of any live or live-attenuated vaccines against infectious diseases (e.g., influenza nasal spray, varicella) within 4 weeks (28 days) of initiation of study treatment
  • Mean resting corrected QTcF \>470 ms, obtained from triplicate ECGs performed at screening.
  • There are no exclusion criteria specific to Modules 1 and 2.
  • Module 3 Specific

Key Trial Info

Start Date :

December 10 2021

Trial Type :

INTERVENTIONAL

Allocation :

ACTUAL

End Date :

November 30 2023

Estimated Enrollment :

45 Patients enrolled

Trial Details

Trial ID

NCT04907851

Start Date

December 10 2021

End Date

November 30 2023

Last Update

March 17 2025

Active Locations (13)

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Page 1 of 4 (13 locations)

1

Wollongong Hospital

Wollongong, New South Wales, Australia, 2500

2

The Alfred Hospital - Alfred Health

Melbourne, Victoria, Australia, 3304

3

Cambridge University Hospital NHS Foundation Trust

Cambridge, United Kingdom, CB2 0XY

4

Beatson West of Scotland Cancer Care

Glasgow, United Kingdom, G12 0YN