Status:
UNKNOWN
Natural History Observational Study of MPS IIIa in SMC
Lead Sponsor:
Samsung Medical Center
Conditions:
Sanfilippo Syndrome A
Eligibility:
All Genders
Brief Summary
To characterize the clinical course of mucopolysaccharidosis type IIIA (MPS IIIA), and identify potential endpoints for future treatment trials.
Eligibility Criteria
Inclusion
- Confirmed diagnosis of MPS IIIA
- Has the ability to comply with protocol requirements, in the opinion of the investigator
Exclusion
- Patient's assent is unattainable, or the patient's parent(s), or patient's legally authorized representative(s) is/are unable to understand the nature, scope, and possible consequences of the study, or do/does not agree to comply with the protocol defined schedule of assessments.
Key Trial Info
Start Date :
June 30 2021
Trial Type :
OBSERVATIONAL
Allocation :
ESTIMATED
End Date :
July 28 2024
Estimated Enrollment :
25 Patients enrolled
Trial Details
Trial ID
NCT04918641
Start Date
June 30 2021
End Date
July 28 2024
Last Update
June 9 2021
Active Locations (0)
Enter a location and click search to find clinical trials sorted by distance.
No Results Found
We couldn’t find results for the location/zipcode entered or within the selected range. Please check your input or adjust your search.