Status:

COMPLETED

Protective Role of Pre-/ Post-biotics on Gut Inflammation, Dysbiosis, and Life Quality in Rett Syndrome (Biotics_RTT)

Lead Sponsor:

Azienda Ospedaliera Universitaria Senese

Collaborating Sponsors:

Kolfarma s.r.l. - Italy

European Institute of Oncology

Conditions:

Rett Syndrome

Dysbiosis

Eligibility:

FEMALE

3+ years

Phase:

NA

Brief Summary

The study will examine the potential efficacy and safety of two pre- and post-biotics on markers for gut inflammation and intestinal microbiota ecology in patients with Rett syndrome. Moreover, this t...

Detailed Description

The gastrointestinal tract is the major site of exposure to environmental molecules where 1) dietary components are chemically transformed by the microbiota, and 2) gut-derived metabolites are dissemi...

Eligibility Criteria

Inclusion

  • Diagnosis of classic/typical Rett syndrome (and proven loss-of-function mutation of the MeCP2 gene) with gastrointestinal dysfunction and/or positive history of epilepsy
  • Female gender (age \> / = 3 years old)
  • Ability to obtain written informed consent from their parent(s)/legal guardian(s)
  • Stable medications for at least 4 weeks prior to the baseline visit.

Exclusion

  • Diagnosis not fitting into the Rett syndrome consensus guidelines
  • Nonpathogenic MECP2 mutation or mutations in non-MECP2 genes (i.e., cyclin-dependent kinase 5, CDKL5; forkhead box protein G1, FOXG1)
  • Male gender
  • Percutaneous endoscopic gastrostomy (PEG) tube
  • Proven hypersensitivity to one or more components of the dietary supplements (X-biotics)
  • Unstable concomitant medications less than 4 weeks prior to enrollment visit.
  • Concomitant antibiotic therapy at the enrollment. In the case of antibiotic therapy, a 4-weeks washout period will be undertaken.
  • Rejection of the informed consent form by the parents/caregivers and/or lack of compliance to the Study procedures.

Key Trial Info

Start Date :

April 1 2022

Trial Type :

INTERVENTIONAL

Allocation :

ACTUAL

End Date :

February 28 2023

Estimated Enrollment :

28 Patients enrolled

Trial Details

Trial ID

NCT05420805

Start Date

April 1 2022

End Date

February 28 2023

Last Update

April 18 2023

Active Locations (1)

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Page 1 of 1 (1 locations)

1

Policlinico "S. Maria alle Scotte" Azienda Ospedaliera Universitaria Senese

Siena, Italy, 53100