Status:

UNKNOWN

The Safety and Efficacy of Zanubrutinib in Refractory/Relapsed Autoimmune Hemolytic Anemia

Lead Sponsor:

Institute of Hematology & Blood Diseases Hospital, China

Conditions:

Refractory/Relapsed Autoimmune Hemolytic Anemia

Eligibility:

All Genders

6-70 years

Phase:

PHASE2

Brief Summary

The sample size of this study is calculated based on Simon's two-stage design. The first stage of the study enrolled a cohort of 12 patients. If after 12 weeks at least 6 patients achieved a response,...

Eligibility Criteria

Inclusion

  • Age from 6 to 70
  • Diagnosis of Coombs-negative AIHA
  • Diagnosis of warm AIHA, mixed AIHA or Evans syndrome.
  • Meets the criteria of relapsed / refractory AIHA
  • ECOG ≤ 3
  • Willing and able to comply with the requirements for this study and written informed consent.

Exclusion

  • Diagnosis of any of the following diseases: Cold agglutinin disease, cold agglutinin syndrome, mixed AIHA, paroxysmal cold hemoglobinuria (PCH).
  • Diagnosis of active stage of connective tissue disease.
  • History of lymphoproliferative tumors or any other malignant.
  • Diagnosis of other inherited or acquired hemolytic diseases.
  • Secondary AIHA caused by drugs or infection.
  • Previously received organ or stem cell transplantation.
  • History of thrombosis or organ infarction.
  • Received rituximab within 8 weeks before enrollment.
  • Previously treated with BTK inhibitor ≥ 2 weeks.
  • Received low-molecular-weight heparin or warfarin within 1 week before enrollment and need to continue the drug treatment.
  • Received CYP3A4 Enzyme Inhibitors or Inducers within 1 week before enrollment and need to continue the drug treatment.
  • Uncontrolled systemic fungal, bacterial, or viral infection (defined as ongoing signs/symptoms related to the infection without improvement despite appropriate antibiotics, antiviral therapy, and/or other treatment), known human immunodeficiency virus (HIV), known evidence of active infectious hepatitis B, and/or known evidence of active hepatitis C.
  • Any severe and/or uncontrolled medical conditions: refractory hypertension, clinically significant cardiac diseases, renal diseases, liver diseases and metabolic diseases, etc.
  • History of mental illness.
  • Participation in another clinical trial within 4 weeks before the start of this trial.
  • Pregnant or breast-feeding patients.
  • Patients considered ineligible for the study by the investigator for reasons other than the above.

Key Trial Info

Start Date :

September 1 2023

Trial Type :

INTERVENTIONAL

Allocation :

ESTIMATED

End Date :

December 31 2025

Estimated Enrollment :

33 Patients enrolled

Trial Details

Trial ID

NCT06021977

Start Date

September 1 2023

End Date

December 31 2025

Last Update

November 29 2023

Active Locations (1)

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Page 1 of 1 (1 locations)

1

Regenerative Medicine Center

Tianjin, Tianjin Municipality, China, 300131