Status:

ACTIVE_NOT_RECRUITING

A Study to Assess Efficacy and Safety of LB54640 in Patients With Hypothalamic Obesity

Lead Sponsor:

Rhythm Pharmaceuticals, Inc.

Conditions:

Hypothalamic Obesity

Eligibility:

All Genders

12+ years

Phase:

PHASE2

Brief Summary

The goal of this study is to determine how well LB54640 works and how safe it is in patients with Hypothalamic Obesity (HO). The study will evaluate the effect of LB54640 on safety, weight reduction, ...

Eligibility Criteria

Inclusion

  • Key
  • Documented evidence of acquired hypothalamic obesity (HO)
  • Age 12 years and older
  • Weight gain associated with the hypothalamic injury and a BMI of ≥30 kg/m2 for patients ≥18 years of age or BMI ≥95th percentile for age and sex for patients \<18 years of age
  • Male and female participants agree to follow study contraception requirements and use a highly effective form of contraception throughout the study and for 90 days after the study
  • Key

Exclusion

  • Weight loss \>2% in the previous 3 months for patients ≥18 years of age or \>2% reduction in BMI for patients \<18 years of age
  • History of major surgical procedure within 30 days
  • HbA1c \>10.9%
  • Fasting glucose level \>270 mg/dL
  • Previous use of MC4R agonists
  • Diagnosis of Prader-Willi syndrome (PWS) or Rapid-onset obesity with hypoventilation, hypothalamic, autonomic dysregulation, neuroendocrine tumor syndrome (ROHHADNET).
  • Diagnosis of severe psychiatric disorders; any suicidal ideation, attempt or behavior
  • History or close family history of skin cancer or melanoma
  • Current clinically significant pulmonary, cardiac, or oncologic disease considered severe enough to interfere with the study and/or confound the results
  • Other protocol defined Inclusion/Exclusion criteria may apply.

Key Trial Info

Start Date :

July 11 2024

Trial Type :

INTERVENTIONAL

Allocation :

ESTIMATED

End Date :

January 31 2026

Estimated Enrollment :

28 Patients enrolled

Trial Details

Trial ID

NCT06046443

Start Date

July 11 2024

End Date

January 31 2026

Last Update

July 22 2025

Active Locations (10)

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Page 1 of 3 (10 locations)

1

Children's Hospital Colorado

Aurora, Colorado, United States, 80045

2

University of Iowa Children's Hospital

Iowa City, Iowa, United States, 52242

3

Tufts Medical Center

Boston, Massachusetts, United States, 02111

4

Columbia University

New York, New York, United States, 10027