Status:

RECRUITING

A Prospective, Non-interventional, Observational Study of Presentation, Treatment Patterns and Outcomes in Atypical Hemolytic Uremic Syndrome Patients

Lead Sponsor:

AstraZeneca

Conditions:

Atypical Hemolytic Uremic Syndrome(aHUS)

Eligibility:

All Genders

Brief Summary

This is a China, non-interventional, observational study and will follow the Good Phar-macoepidemiology Practices guidelines. This study will enrol paediatric and adult patients diagnosed with aHUS w...

Eligibility Criteria

Inclusion

  • Participants are eligible to be included in the study. Age
  • Patients of any age, who are diagnosed as aHUS by a professional physician (first epi-sode or relapse).
  • Type of Patient and Disease Characteristics
  • Evidence of TMA, including thrombocytopenia, evidence of hemolysis, and kidney dys-function, based on the following laboratory findings, should be recorded within 2 weeks time frame:
  • Platelet count \< 150,000 per microliter (μL), and
  • Mechanic hemolytic anemia evident by LDH ≥ 1.5 × upper limit of normal (ULN), and hemoglobin ≤ lower limit of normal (LLN) for age and gender and
  • Serum creatinine level ≥ ULN in adults (≥18 years of age), or ≥ 97.5th percentile for age at screening in children (patients who require dialysis for acute kidney injury are also eligi-ble).
  • Gender: Male and/or female. Informed Consent
  • Willing and able to give written informed consent and comply with the study visit schedule as described in Section 6.2.1. For patients \< 18 years of age, patient's legal guardian must be willing and able to give written informed consent and the patient must be willing to give written informed assent (if applicable as determined by the central.

Exclusion

  • Participants are excluded from the study if any of the following criteria apply:
  • Medical Conditions
  • Patients who were diagnosed with HUS only due to Shiga toxin-producing Escherichia coli (STEC).
  • Patients who were diagnosed with TTP (ADAMTS13 activity \<10%). Other Exclusions
  • Unable to give written informed consent.
  • Any medical or psychological condition that, in the opinion of the Investigator, could increase the risk to the participant by participating in the study or confound the outcome of the study.

Key Trial Info

Start Date :

January 15 2024

Trial Type :

OBSERVATIONAL

Allocation :

ESTIMATED

End Date :

December 31 2027

Estimated Enrollment :

1070 Patients enrolled

Trial Details

Trial ID

NCT06099236

Start Date

January 15 2024

End Date

December 31 2027

Last Update

December 19 2025

Active Locations (37)

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Page 1 of 10 (37 locations)

1

Research Site

Beijing, Beijing Municipality, China

2

Research Site

Luzhou, Sichuan, China

3

Research Site

Baoding, China

4

Research Site

Beijing, China