Status:

WITHDRAWN

Defibrotide Prophylaxis of Transplant Associated-Thrombotic Microangiopathy for Neuroblastoma

Lead Sponsor:

University of California, San Francisco

Collaborating Sponsors:

Jazz Pharmaceuticals

Conditions:

Transplant-Associated Thrombotic Microangiopathy

Neuroblastoma

Eligibility:

All Genders

1-18 years

Phase:

PHASE2

Brief Summary

This phase II trial tests how well defibrotide works in preventing transplant-associated thrombotic microangiopathy (TA-TMA) in patients with high-risk neuroblastoma undergoing tandem transplants (hem...

Detailed Description

PRIMARY OBJECTIVE: I. To determine if administration of prophylactic defibrotide sodium (defibrotide) will prevent the development of TA-TMA in participants with high-risk neuroblastoma receiving tan...

Eligibility Criteria

Inclusion

  • Age: 1 - \< 18 years old.
  • Participants must have high-risk neuroblastoma according to Children's Oncology Group (COG) risk classification at the time of initial diagnosis. Participants who were initially considered low or intermediate risk, but then reclassified as high risk are also eligible.
  • Participants may have had salvage therapies (i.e., meta-iodobenzylguanidine (MIBG), dinutuximab) after induction but cannot have progressive disease at start of 4.
  • Planned tandem transplants with conditioning with cyclophosphamide-thiotepa and carboplatin-etoposide-melphalan on, or as per, NCT03126916 (ANBL1531) or other tandem-containing COG high-risk neuroblastoma trials.
  • Participants may be enrolled in upfront neuroblastoma protocol, but this is not required.
  • Upfront MIBG or other therapies is not a contraindication.
  • Organ function per institutional standard of care (SOC) guiding clearance for autologous HSCT.
  • Written informed consent (and assent when applicable) obtained from participant or participant's legal representative and ability for subject to comply with the requirements of the study.

Exclusion

  • Life expectancy \< 6 months.
  • Pregnant, breastfeeding, or unwilling to practice birth control during participation in the study.
  • Presence of a condition or abnormality that in the opinion of the Investigator would compromise the safety of the patient or the quality of the data.
  • Known bleeding diathesis or bleeding risk deemed by the treating physician to be a contraindication to administration of defibrotide or on concomitant therapeutic anticoagulation. Administration of heparin and/or alteplase for central line maintenance is allowed.

Key Trial Info

Start Date :

August 1 2024

Trial Type :

INTERVENTIONAL

Allocation :

ACTUAL

End Date :

May 31 2027

Estimated Enrollment :

Patients enrolled

Trial Details

Trial ID

NCT06182410

Start Date

August 1 2024

End Date

May 31 2027

Last Update

August 7 2024

Active Locations (0)

Enter a location and click search to find clinical trials sorted by distance.

Page 1 of 0 (0 locations)

No Results Found

We couldn’t find results for the location/zipcode entered or within the selected range. Please check your input or adjust your search.