Status:

RECRUITING

Charcot-Marie-Tooth Disease (CMT) Biological Sample Collection for IPSC Generation and Biobanking

Lead Sponsor:

New York Stem Cell Foundation Research Institute

Collaborating Sponsors:

Charcot-Marie-Tooth Association

Conditions:

Charcot-Marie-Tooth Disease

Healthy

Eligibility:

All Genders

5+ years

Brief Summary

The New York Stem Cell Foundation (NYSCF) Research Institute is performing this research to accelerate Charcot-Marie-Tooth disease research and drug development by using cells from the body (such as s...

Detailed Description

Researchers at the New York Stem Cell Foundation (NYSCF) Research Institute study diverse diseases, conditions, and traits by creating stem cells from biological samples. These "pluripotent" stem cell...

Eligibility Criteria

Inclusion

  • Age 5 years or older.
  • Diagnosis of Charcot-Marie-Tooth (CMT) disease or healthy controls.
  • Adults must provide written informed consent unless physical limitations preclude signing.
  • Minors undergoing skin collection for research purposes must have a CMT diagnosis and must participate with parent/guardian consent.
  • Minors undergoing blood and/or saliva collection for research purposes or who transfer biological samples from a procedure outside the research may have a CMT diagnosis or serve as a healthy control and may participate with parent/guardian consent.

Exclusion

  • Wards of the state.
  • For prospective skin samples: history of keloid formation, coagulation disorder, allergy to the anesthetic, or anticoagulation use that precludes sample collection.
  • For prospective blood samples: coagulation disorder or other medical conditions that increase the risks associated with blood collection.
  • For all prospective sample collections: Subjects who refuse to adhere to NYSCF's and/or a collaborating site's safety protocols will be excluded. Subjects with an AIDS diagnosis and CD4 count of less than 200 cells per microliter of blood will be excluded due to increased risk of infection.

Key Trial Info

Start Date :

September 22 2022

Trial Type :

OBSERVATIONAL

Allocation :

ESTIMATED

End Date :

September 22 2025

Estimated Enrollment :

50 Patients enrolled

Trial Details

Trial ID

NCT06203093

Start Date

September 22 2022

End Date

September 22 2025

Last Update

March 3 2025

Active Locations (1)

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New York Stem Cell Foundation Research Institute

New York, New York, United States, 10019