Status:

RECRUITING

Study of Subretinally Injected AAVB-081 in Patients With Usher Syndrome Type IB (USH1B) Retinitis Pigmentosa

Lead Sponsor:

AAVantgarde Bio Srl

Conditions:

Usher Syndrome, Type 1B

Eligibility:

All Genders

18-50 years

Phase:

PHASE1

PHASE2

Brief Summary

The purpose of the 081-101 study is to evaluate the safety and tolerability of a single subretinal injection of AAVB-081 in USH1B patients with retinitis pigmentosa due to a mutation in the MYO7A gene...

Eligibility Criteria

Inclusion

  • Molecular diagnosis of USB1B due to MYO7A mutation
  • Willingness to adhere to protocol per informed consent

Exclusion

  • Unwillingness to meet the requirements of the study
  • Participation in a clinical study with an Investigation Product in the past 6 months
  • Previous participation in another Gene Therapy trial
  • Any condition that would preclude subretinal surgery
  • Complicating ocular and/or systemic diseases

Key Trial Info

Start Date :

July 2 2024

Trial Type :

INTERVENTIONAL

Allocation :

ESTIMATED

End Date :

July 1 2029

Estimated Enrollment :

15 Patients enrolled

Trial Details

Trial ID

NCT06591793

Start Date

July 2 2024

End Date

July 1 2029

Last Update

May 2 2025

Active Locations (3)

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Page 1 of 1 (3 locations)

1

University of Campania Luigi Vanvitelli

Naples, Italy

2

Moorfields Eye Hospital

London, United Kingdom

3

Retina Clinic London

London, United Kingdom