Status:

COMPLETED

A Study to Evaluate the Efficacy and Safety of Oral HRS-5965 in Adult Paroxysmal Nocturnal Hemoglobinuria (PNH) Patients Who Are Naive to Complement Inhibitor Therapy

Lead Sponsor:

Chengdu Suncadia Medicine Co., Ltd.

Conditions:

Paroxysmal Nocturnal Hemoglobinuria

Eligibility:

All Genders

18+ years

Phase:

PHASE3

Brief Summary

A study of the efficacy and safety of HRS-5965 capsules compared to eculizumab for 24 weeks in patients with PNH.

Eligibility Criteria

Inclusion

  • Diagnosis of PNH confirmed by flow cytometry with clone size \> 10%.
  • Have not received complement inhibitor therapy;
  • LDH \> 1.5\*ULN at screening.
  • Hemoglobin level \< 10 g/dL at screening.

Exclusion

  • Known or suspected hereditary or acquired complement deficiency;
  • Patients with laboratory evidence of bone marrow failure (reticulocytes \<100x109/L; platelets \<30x109/L; neutrophils \<0.5x109/L);
  • Presence or suspicion of a systemic active bacterial, viral, or fungal infection (based on judgment of the investigator) within 2 weeks prior to the first dose of HRS-5965;
  • History of infection with capsular bacteria (e.g., meningococcus, pneumococcus, etc.)
  • Positive of HIV, HBsAg or HCVAb.

Key Trial Info

Start Date :

October 25 2024

Trial Type :

INTERVENTIONAL

Allocation :

ACTUAL

End Date :

July 31 2025

Estimated Enrollment :

76 Patients enrolled

Trial Details

Trial ID

NCT06593938

Start Date

October 25 2024

End Date

July 31 2025

Last Update

September 11 2025

Active Locations (2)

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Page 1 of 1 (2 locations)

1

Peking Union Medical College Hospital, Chinese Academy of Medical Sciences

Beijing, Beijing Municipality, China, 100730

2

The Blood Disease Hospital of the Chinese Academy of Medical Sciences

Tianjin, Tianjin Municipality, China, 300020

A Study to Evaluate the Efficacy and Safety of Oral HRS-5965 in Adult Paroxysmal Nocturnal Hemoglobinuria (PNH) Patients Who Are Naive to Complement Inhibitor Therapy | DecenTrialz