Status:

RECRUITING

An Open Label Trial to Evaluate the Efficacy and Safety of PRAX-628 in Adults With Focal Onset or Tonic-Clonic Seizures

Lead Sponsor:

Praxis Precision Medicines

Conditions:

Focal Onset Seizure

Primary Generalized Epilepsy

Eligibility:

All Genders

18-75 years

Phase:

PHASE2

Brief Summary

An Open Label Clinical Trial to Evaluate the Efficacy and Safety of PRAX-628 in Adult Patients With Focal Onset or Primary Generalized Tonic-Clonic Seizures

Detailed Description

An open label clinical trial to evaluate the efficacy and safety of PRAX-628 in adult patients with focal onset or primary generalized tonic-clonic seizures who can attest to concurrently taking at le...

Eligibility Criteria

Inclusion

  • A diagnosis of focal onset seizures or idiopathic generalized tonic clonic seizures.
  • Evidence by computed tomography (CT) or magnetic resonance imaging (MRI) in the past that has ruled out a progressive cause of epilepsy.
  • Participant must have been receiving stable doses of allowable ASMs (a minimum of 1 and a maximum of 3 ASMs).
  • Participant and/or caregiver (if applicable) self-reports at least 2 countable focal onset seizures per month for focal onset patients, or 1 countable generalized tonic-clonic seizure per month in the 3 months immediately prior to the Screening/Observation Period for PGTCS patients.

Exclusion

  • History of pseudo or psychogenic seizures, or cluster seizures only, within the 12-month period preceding study entry where the individual seizures cannot be counted, or an episode of convulsive status epilepticus requiring hospitalization and intubation in the 12 months prior to Screening.
  • Planned epilepsy surgery during the course of the clinical trial.
  • History of neurosurgery for seizures \<1 year prior to enrollment, or radiosurgery \<2 years prior to enrollment.
  • Schizophrenia and obsessive-compulsive disorder, or other serious mental health disorders.
  • Active suicidal plan/intent in the past 6 months, or a history of suicide attempt in the last 2 years, or more than 1 lifetime suicide attempt.
  • Participants with a history of malignancy, myeloproliferative or lymphoproliferative disorders within the past 5 years are excluded.
  • History of cardiac disease(s)/cardiac conduction disorders/or cardiac structural abnormality(ies).
  • Is pregnant or breastfeeding at the time of Screening, or has a positive serum pregnancy test at Screening or is planning to become pregnant during the clinical trial or within 14 days of the last study drug dose.
  • Has received any other experimental or investigational drug, device or other therapy within 30 days or 5 half-lives (whichever is longer) prior to Screening, or any prior use of gene therapy.
  • Vigabatrin: Use in the last 5 years without stable visual fields tested twice over the 12 months after the last dose of vigabatrin.
  • Felbamate: If used as a concomitant ASM, patients must be on felbamate for at least 2 years, with a stable dose for 2 months prior to Screening. If a patient received felbamate in the past, it must have been discontinued 2 months prior to Screening.

Key Trial Info

Start Date :

January 10 2025

Trial Type :

INTERVENTIONAL

Allocation :

ESTIMATED

End Date :

July 1 2025

Estimated Enrollment :

50 Patients enrolled

Trial Details

Trial ID

NCT06908356

Start Date

January 10 2025

End Date

July 1 2025

Last Update

April 3 2025

Active Locations (11)

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Page 1 of 3 (11 locations)

1

Praxis Research Site

Phoenix, Arizona, United States, 85032

2

Praxis Research Site

Miami Lakes, Florida, United States, 30116

3

Praxis Research Site

Bethesda, Maryland, United States, 20817

4

Praxis Research Site

Chesterfield, Missouri, United States, 63005