Status:

RECRUITING

A Study to Investigate the Efficacy and Safety of Bemdaneprocel in Adults Who Have Parkinson's Disease

Lead Sponsor:

BlueRock Therapeutics

Collaborating Sponsors:

Bayer

Conditions:

Parkinsons Disease (PD)

Eligibility:

All Genders

45-75 years

Phase:

PHASE3

Brief Summary

Study BRT-DA01-301 is a Phase 3 multicenter, randomized, sham surgery-controlled, double-blind study to assess efficacy and safety of bemdaneprocel in approximately 102 adults with Parkinson's Disease...

Detailed Description

The BRT-DA01-301 study is a Phase 3, multicenter, randomized, sham surgery-controlled, double-blind study involving approximately 102 participants with Parkinson's Disease (PD). Participants will be r...

Eligibility Criteria

Inclusion

  • Diagnosis of clinically established PD as defined by the International Parkinson and Movement Disorders Society
  • Individual of any sex ≥45 to ≤75 years of age at informed consent
  • Robust and clear response to DA therapy as defined by MDS-UPDRS Part III
  • ≥4 and \<12 years from time of PD diagnosis at informed consent
  • Must demonstrate responsiveness to levodopa therapy
  • Receiving medical therapy for the treatment of PD symptoms
  • ≥2.5 hours of daily OFF-time
  • Vaccinated per current national guidelines or local practice for patients with altered immunocompetence

Exclusion

  • PD presenting with recurrent falls
  • Diagnosis of primary mitochondrial disorder, epilepsy, stroke, multiple sclerosis, or clinical features suggestive of a neurodegenerative disease other than PD, including multiple system atrophy, progressive supranuclear palsy, corticobasal degeneration, or Lewy body dementia
  • Any current or relevant previous history of serious, severe, or unstable physical, neurological, or psychiatric illness that may interfere with study participation, participant's safety, or assessment of endpoints per investigator's judgment
  • History of gene therapy or cell therapy
  • Prior treatment with intrajejunal or subcutaneous infusion therapies for PD
  • Prior surgical or radiation therapy to the brain, including deep brain stimulation (DBS) and lesion therapy, or prior history of intradural spinal cord surgery
  • Contraindication to surgery, general anesthesia, cell therapy, immunosuppression, or other required drugs, or anything that prevents use of PET or MRI
  • Any active infection (including but not limited to HIV, HCV, HBV, CMV, syphilis, or tuberculosis) or condition that, in the opinion of the investigator could put the participant at significant risk from immunosuppression or impact the participant's ability to perform study assessments
  • Current or previously active malignant disease within the past 5 years
  • Chronic immunosuppressive therapy
  • Receipt of another investigational therapy within 5 half-lives of the active treatment
  • Pregnancy or breastfeeding

Key Trial Info

Start Date :

June 17 2025

Trial Type :

INTERVENTIONAL

Allocation :

ESTIMATED

End Date :

March 1 2032

Estimated Enrollment :

102 Patients enrolled

Trial Details

Trial ID

NCT06944522

Start Date

June 17 2025

End Date

March 1 2032

Last Update

December 4 2025

Active Locations (18)

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Page 1 of 5 (18 locations)

1

UCLA NeuroTranslational Research Center

Los Angeles, California, United States, 90095

2

University of Colorado Hospital - Neurology Clinic

Aurora, Colorado, United States, 80045

3

MedStar Georgetown University Hospital

Washington D.C., District of Columbia, United States, 20007

4

University of Miami Health System - Neurology

Miami, Florida, United States, 33136