Status:

RECRUITING

Phase 2a Study of VX-407 in Participants With ADPKD Who Have a Subset of PKD1 Gene Variants (AGLOW)

Lead Sponsor:

Vertex Pharmaceuticals Incorporated

Conditions:

Autosomal Dominant Polycystic Kidney Disease (ADPKD)

Eligibility:

All Genders

18-65 years

Phase:

PHASE2

Brief Summary

The purpose of the study is to evaluate the effect of VX-407 on height-adjusted total kidney volume (htTKV), safety, tolerability, and pharmacokinetics (PK) of VX-407.

Eligibility Criteria

Inclusion

  • Key
  • A pre-existing diagnosis of ADPKD as defined in the protocol
  • Willing and able to comply with scheduled visits and other study procedures
  • Participants with ADPKD with Mayo imaging classification (MIC) status of 1B (with htTKV ≥250 mL/m), 1C, 1D, or 1E confirmed by abdominal MRI obtained during screening
  • Estimated glomerular filtration rate (eGFR) greater than or equal to (≥) 25 milliliter per minute (mL/min)/1.73 square meter (m\^2)
  • Key

Exclusion

  • History of kidney disease other than ADPKD that in the opinion of the investigator would independently impact the natural history of ADPKD
  • History of solid organ or bone marrow transplantation or nephrectomy
  • Ongoing renal replacement therapy or planning to start renal replacement therapy within 12 months of screening
  • Other protocol defined Inclusion/Exclusion criteria will apply.

Key Trial Info

Start Date :

November 19 2025

Trial Type :

INTERVENTIONAL

Allocation :

ESTIMATED

End Date :

December 31 2027

Estimated Enrollment :

24 Patients enrolled

Trial Details

Trial ID

NCT07161037

Start Date

November 19 2025

End Date

December 31 2027

Last Update

December 18 2025

Active Locations (21)

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Page 1 of 6 (21 locations)

1

Alabama Kidney Research

Alabaster, Alabama, United States, 35007

2

Kaiser Permanente Los Angeles Medical Center

Los Angeles, California, United States, 90027

3

UCSF Clinical Research Center at Parnassus

San Francisco, California, United States, 94143

4

Nephrology & Hypertension Associates, PC

Middlebury, Connecticut, United States, 06762