Actively Recruiting

Early Phase 1
Age: 12Years - 80Years
All Genders
NCT04744116

Addition of Cord Blood Tissue-Derived Mesenchymal Stromal Cells to Ruxolitinib for the Treatment of Steroid-Refractory Acute Graft Versus Host Disease

Led by M.D. Anderson Cancer Center · Updated on 2026-05-05

24

Participants Needed

1

Research Sites

580 weeks

Total Duration

On this page

Sponsors

M

M.D. Anderson Cancer Center

Lead Sponsor

N

National Cancer Institute (NCI)

Collaborating Sponsor

AI-Summary

What this Trial Is About

This early phase I trial is to find out the effect of adding cord blood tissue-derived mesenchymal stromal cells (cb-MSCs) to ruxolitinib in treating patients with acute graft versus host disease that does not respond to steroid therapy (steroid-refractory). Ruxolitinib may stop the growth of cancer cells by blocking some of the enzymes needed for cell growth. cb-MSCs are a type of tissue helper cell that can be removed from donated umbilical cord blood tissue and grown into many different cell types that can be used to treat cancer and other disease, such as graft versus host disease. This trial aims to learn if adding cb-MSCs to ruxolitinib may help control steroid-refractory acute graft versus host disease.

CONDITIONS

Official Title

Addition of Cord Blood Tissue-Derived Mesenchymal Stromal Cells to Ruxolitinib for the Treatment of Steroid-Refractory Acute Graft Versus Host Disease

Who Can Participate

Age: 12Years - 80Years
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Participants between the ages of 12 years and 80 years (inclusive)
  • Steroid refractory grades II-IV acute GVHD of the lower GI tract or liver after allogeneic HCT or donor lymphocyte infusion
  • No improvement after methylprednisolone at ≥ 2.0 mg/kg/day for at least 7 days, or progressive symptoms after 3 days, or flare while on systemic steroids
  • Biopsy suggesting GVHD (repeat biopsy not required for enrollment)
  • Karnofsky/Lansky Performance score of at least 30 at study entry
  • Women of childbearing potential must be non-pregnant, not breastfeeding, and use adequate contraception
  • Male patients must use adequate contraception
  • Ability to provide written informed consent (or assent if appropriate)
Not Eligible

You will not qualify if you...

  • De novo chronic GVHD
  • Isolated acute GVHD of the skin
  • Secondary systemic therapy for acute GVHD with ruxolitinib started more than 96 hours before study therapy
  • Primary treatment with agents other than alpha-1 antitrypsin, glucocorticoids, or ruxolitinib
  • Uncontrolled infections defined by signs of progression such as hemodynamic instability, new symptoms, worsening signs or imaging
  • Cognitive impairments or serious unstable medical or psychiatric conditions affecting safety or consent
  • Significant supplemental oxygen need (>6 L by nasal cannula)
  • Known allergy to bovine or porcine products

AI-Screening

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Trial Site Locations

Total: 1 location

1

M D Anderson Cancer Center

Houston, Texas, United States, 77030

Actively Recruiting

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Research Team

P

Partow Kebriaei, MD

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

RANDOMIZED

Model

PARALLEL

Primary Purpose

TREATMENT

Number of Arms

3

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