Long-term efficacy of miglustat in paediatric patients with Niemann-Pick disease type C.
Y H Chien, S F Peng, C C Yang...
https://pubmed.ncbi.nlm.nih.gov/22476655Completed
Phase 3
All Genders
ID01760564
Application of Miglustat in Patients With Niemann-Pick Type C
Led by National Taiwan University Hospital · Updated on 2013-01-04
5
Participants Needed
1
Research Sites
N/A
Total Duration
On this page
AI-Summary
What this Trial Is About
To evaluate the changes in cognitive function after miglustat treatment in Niemann-Pick type C patients.
CONDITIONS
Official Title
Application of Miglustat in Patients With Niemann-Pick Type C
Who Can Participate
All Genders
Eligibility Criteria
You may qualify if you...
- Confirm diagnosis of Niemann-Pick C disease
- Symptomatic including motor or mental symptoms
You will not qualify if you...
- Unknown severe diarrhea for more than 7 day
- Allergy to miglustat
Trial Site Locations
Total: 1 location
1
National Taiwan University Hospital
Taipei, Taiwan
Status Unknown
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How is the study designed?
Study Type
INTERVENTIONAL
Masking
NONE
Allocation
NA
Model
SINGLE_GROUP
Primary Purpose
TREATMENT
Number of Arms
1
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