Actively Recruiting

Age: 0 - 18Years
All Genders
ID04338048

Autosomal Dominant Polycystic Kidney Disease (ADPKD) Study

Led by Children's Hospital of Philadelphia · Updated on 2025-06-13

300

Participants Needed

4

Research Sites

N/A

Total Duration

On this page

Sponsors

C

Children's Hospital of Philadelphia

Lead Sponsor

N

National Institutes of Health (NIH)

Collaborating Sponsor

AI-Summary

What this Trial Is About

Autosomal Dominant Polycystic Kidney Disease (ADPKD) is the most common inherited cause of kidney failure and has long been seen as a disease that starts in adulthood. Recent understanding shows the disease begins in childhood, but there is limited data on how it progresses during these early years. This study aims to better understand ADPKD and other related liver and kidney fibrocystic diseases, while also providing accessible online resources about these conditions for everyone. Participants diagnosed with ADPKD or similar dominant hepato/renal fibrocystic diseases will allow the study team to access their medical records, including clinic notes, lab results, and physician reports. There are no required visits to a study center. Medical information will be entered into a clinical database for these diseases, with personal identifiers removed to maintain privacy. Data collection includes initial and follow-up entries over the study period. Participants will contribute medical data for up to 10 years or until they decide to leave the study. The research team will monitor the information collected in the Hepato/Renal Fibrocystic Diseases clinical database. This approach helps researchers learn more about the clinical course of ADPKD in children without requiring in-person visits, minimizing burden for participants and families.

CONDITIONS

Brief Title

Autosomal Dominant Polycystic Kidney Disease (ADPKD) Study

Who Can Participate

Age: 0 - 18Years
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Diagnosis of ADPKD confirmed by clinical information, imaging, biopsy, autopsy, or genetic testing
  • Age 18 years or younger
Not Eligible

You will not qualify if you...

  • Diagnosis of Autosomal Recessive Polycystic Kidney Disease (ARPKD)
  • Presence of urinary tract malformations or major congenital anomalies suggesting other recessive hepato-renal fibrocystic diseases

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Your Study Journey

Screening

Duration - 2 to 4 weeks

Participants are screened for eligibility to participate in the trial.

No clinic visits are required; eligibility is determined through medical records review.

Surveillance

Duration - Up to 10 years

Participants' past, current, and future medical information related to ADPKD is collected and entered into a clinical database.

No clinic visits are required; data collection is based on medical records and reports.

Trial Site Locations

Total: 4 locations

1

Children's National Hospital

Washington D.C., District of Columbia, United States, 20010

Actively Recruiting

2

Mayo Clinic

Rochester, Minnesota, United States, 55902

Actively Recruiting

3

Cohen Children's Medical Center

New Hyde Park, New York, United States, 11042

Enrolling by Invitation

4

Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, United States, 19146

Actively Recruiting

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Research Team

J

Jasmine Jaber, MS

How is the study designed?

Study Type

OBSERVATIONAL

Masking

N/A

Allocation

N/A

Model

N/A

Primary Purpose

N/A

Number of Arms

0

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