Actively Recruiting

Phase 3
Age: 1Month - 18Years
All Genders
NCT07224581

Beeline: A Phase 3 Study in GRIN-related Neurodevelopmental Disorder

Led by GRIN Therapeutics, Inc. · Updated on 2026-02-27

100

Participants Needed

17

Research Sites

129 weeks

Total Duration

On this page

Sponsors

G

GRIN Therapeutics, Inc.

Lead Sponsor

A

Aziende Chimiche Riunite Angelini Francesco S.p.A

Collaborating Sponsor

AI-Summary

What this Trial Is About

The Phase 3 portion of Study RAD-GRIN-101 is a multinational, multicenter, randomized, double-blind, placebo-controlled trial followed by an open-label extension to evaluate the efficacy and safety of radiprodil in participants with GRIN-related neurodevelopmental disorder (GRIN-NDD) with a gain-of-function (GoF) genetic variant. This study will enroll two cohorts: one cohort of participants with a minimal number of countable motor seizures (with or without behavioral symptoms) (Phase 3 Cohort 1: Qualifying Seizures Cohort); and a second cohort with disease symptoms but no seizures or fewer seizures than required for the Qualifying Seizures Cohort (Phase 3 Cohort 2: Without Qualifying Seizures Auxiliary Cohort). Participants in each cohort will be randomized 1:1 to receive active drug (radiprodil) or matching placebo (Part A). Following completion of Part A, all eligible participants (including those previously on placebo) may continue into the open-label extension period (Part B) to receive radiprodil. The placebo-controlled portion is expected to be approximately 16 weeks for participants in Phase 3 Cohort 1 and 28 weeks for participants in Phase 3 Cohort 2. The study will evaluate the effect of radiprodil on seizures and non-seizure symptoms and assess safety.

CONDITIONS

Official Title

Beeline: A Phase 3 Study in GRIN-related Neurodevelopmental Disorder

Who Can Participate

Age: 1Month - 18Years
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Diagnosed with GRIN-NDD with GRIN1, GRIN2A, GRIN2B, or GRIN2D gene variants causing gain-of-function of the NMDA receptor
  • For Phase 3 Cohort 1: Experiencing at least 1 countable motor seizure per week and at least 4 countable motor seizures during screening
  • History of inadequate response to at least 2 standard antiseizure medications
  • For Phase 3 Cohort 2: Significant neurodevelopmental symptoms and a GRIN-CGI-S score of 4 or higher
  • On stable doses of standard antiseizure medications for at least 4 weeks prior to screening and remain stable during participation
  • On stable nonpharmacological treatments such as ketogenic diet and remain stable during participation
  • For Part B: Completed Part A and deemed eligible to continue by investigator and sponsor
Not Eligible

You will not qualify if you...

  • Clinically relevant medical, neurologic, psychiatric condition, or behavioral disorder that would jeopardize safe participation or study drug administration
  • Receiving more than 4 standard antiseizure medications at screening
  • Body weight less than 5 kg at screening
  • For Part B: Clinically relevant medical, neurologic, psychiatric condition, or behavioral disorder that would jeopardize safe participation or study drug administration

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Trial Site Locations

Total: 17 locations

1

UCLA Clinical & Translational Research Center

Los Angeles, California, United States, 90095

Actively Recruiting

2

Lucile Packard Children's Hospital

Palo Alto, California, United States, 94304

Actively Recruiting

3

Children's Hospital Colorado - Anschutz Medical Campus

Aurora, Colorado, United States, 80045

Actively Recruiting

4

Children's National Hospital

Washington D.C., District of Columbia, United States, 20010

Actively Recruiting

5

Nicklaus Children's Hospital

Miami, Florida, United States, 33155

Actively Recruiting

6

Pediatric Neurology and Epilepsy

Winter Park, Florida, United States, 32789

Actively Recruiting

7

Iowa Health Care - Pediatric Neurology & Specialty Clinic

Iowa City, Iowa, United States, 52242

Actively Recruiting

8

Boston Children's Hospital

Boston, Massachusetts, United States, 02115

Actively Recruiting

9

Northeast Regional Epilepsy Group (NEREG) - Hackensack

Hackensack, New Jersey, United States, 07601

Actively Recruiting

10

Columbia University - Harkness

New York, New York, United States, 10032

Actively Recruiting

11

Duke Health-Duke Children's Hospital & Health Center

Durham, North Carolina, United States, 27705

Actively Recruiting

12

Cincinnati Children's Hospital Medical Center

Cincinnati, Ohio, United States, 45229

Not Yet Recruiting

13

Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, United States, 19104

Actively Recruiting

14

Child Neurology Consultants of Austin - South Austin

Austin, Texas, United States, 78757

Actively Recruiting

15

The University of Texas Southwestern Medical Center (UTSW)

Dallas, Texas, United States, 75390

Not Yet Recruiting

16

UTHealth Houston

Houston, Texas, United States, 77030

Actively Recruiting

17

Seattle Children's Hospital

Seattle, Washington, United States, 98105

Actively Recruiting

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Research Team

C

Clinical Operations

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

TRIPLE

Allocation

RANDOMIZED

Model

PARALLEL

Primary Purpose

TREATMENT

Number of Arms

2

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Beeline: A Phase 3 Study in GRIN-related Neurodevelopmental Disorder | DecenTrialz