Actively Recruiting

Phase 1
Age: 0 - 21Years
All Genders
NCT04318678

CD123-Directed T-Cell Therapy for Acute Myelogenous Leukemia (CATCHAML)

Led by St. Jude Children's Research Hospital · Updated on 2026-03-30

108

Participants Needed

2

Research Sites

521 weeks

Total Duration

On this page

AI-Summary

What this Trial Is About

The CD123-CAR T-cell therapy is a new treatment that is being investigated for treatment of AML/myelodysplastic syndrome (MDS), T- or B- acute lymphoblastic leukemia (ALL) or blastic plasmacytoid dendritic cell neoplasia (BPDCN). The purpose of this study is to find the maximum (highest) dose of CD123-CAR T cells that is safe to give to these patients. This would include studying the side effects of the chemotherapy, as well as the CD123-CAR T-cell product on the recipient's body, disease and overall survival. Primary Objective: * To determine the safety of one intravenous infusion of escalating doses of autologous, CD123-CAR T cells in patients (≤21 years) with recurrent/refractory CD123+ disease (AML/MDS, B-ALL, T-ALL or BPDCN) after lymphodepleting chemotherapy. * To determine the safety of an intravenous infusion of escalating doses of donor derived, CD123-CAR T cells in patients (≤21 years) with recurrent/refractory CD123+ disease (AML/MDS, B-ALL, T-ALL, BPDCN or MPAL) after lymphodepleting chemotherapy. Secondary Objectives \- To evaluate the antileukemia activity of CD123-CAR T cells. Exploratory Objectives * To assess the immunophenotype, clonal structure and endogenous repertoire of CD123-CAR T cells and unmodified T cells * To characterize the cytokine profile in the peripheral blood and CSF after treatment with CD123-CAR T cells * To characterize tumor cells post CD123-CAR T-cell therapy * To compare in vivo properties of donor-derived versus autologous CD123- CAR T cells

CONDITIONS

Official Title

CD123-Directed T-Cell Therapy for Acute Myelogenous Leukemia (CATCHAML)

Who Can Participate

Age: 0 - 21Years
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Age 21 years or younger
  • Relapsed or refractory CD123-positive AML/MDS, B-ALL, T-ALL, or BPDCN
  • Relapsed AML/MDS after first complete remission or refractory disease after 2 induction chemotherapy cycles
  • Relapsed or refractory CD123-positive B-ALL that is CD19 negative/dim or unsuitable for CD19 therapies
  • Relapsed or refractory CD123-positive T-ALL
  • Relapsed or refractory BPDCN after front-line therapy failure
  • Estimated life expectancy greater than 12 weeks (for procurement phase) or greater than 8 weeks (for treatment phase)
  • Karnofsky or Lansky performance score of 50 or higher
  • Clinically recovered from prior allogeneic stem cell transplant with no active graft-versus-host disease and no donor lymphocyte infusion within 28 days prior to apheresis or infusion
  • Identified suitable hematopoietic cell transplant donor
  • For females of child-bearing age: not pregnant, not lactating, with negative pregnancy test within 7 days prior to enrollment
  • Eligible for or have completed autologous apheresis
  • Detectable CD123-positive disease at treatment start
  • Adequate cardiac, renal, and pulmonary function as defined in the protocol
  • Recovered from significant non-hematologic toxicities from previous therapies
  • Agreement to use birth control if sexually active until 3 months after T-cell infusion
Not Eligible

You will not qualify if you...

  • Known primary immunodeficiency
  • History of HIV infection
  • Severe uncontrolled bacterial, viral, or fungal infection
  • History of hypersensitivity to murine protein-containing products
  • Acute promyelocytic leukemia (APL, t(15;17))
  • Contraindication to lymphodepleting chemotherapy with fludarabine and cyclophosphamide
  • History of severe hypersensitivity to cornstarch or hydroxyethyl starch
  • Receiving systemic steroids above 0.5 mg/kg/day methylprednisolone equivalent within 7 days before infusion
  • Receiving systemic therapy within 14 days before infusion that may interfere with CD123-CAR T cells
  • Receiving rituximab within 30 days before infusion
  • Receiving intrathecal chemotherapy within 7 days before infusion
  • Active central nervous system disease

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

1
2
3
+1

Trial Site Locations

Total: 2 locations

1

St Jude Children's Research Hospital

Memphis, Tennessee, United States, 38105

Actively Recruiting

2

St. Jude Children's Research Hospital

Memphis, Tennessee, United States, 38105

Actively Recruiting

Loading map...

Research Team

S

Swati Naik, MD

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NON_RANDOMIZED

Model

SINGLE_GROUP

Primary Purpose

TREATMENT

Number of Arms

2

Not the Right Trial for You?

Explore thousands of other clinical trials that might be a better match.
Sign up to get personalized trial recommendations delivered to your inbox.

Already have an account? Log in here