Actively Recruiting

Phase 1
Phase 2
Age: 18Years +
All Genders
ID04047641

A Combination of Cladribine, Idarubicin, Cytarabine, and Quizartinib for Treating Newly Diagnosed or Relapsed/Refractory Acute Myeloid Leukemia and High-Risk Myelodysplastic Syndrome

Led by M.D. Anderson Cancer Center · Updated on 2025-12-17

80

Participants Needed

1

Research Sites

N/A

Total Duration

On this page

Sponsors

M

M.D. Anderson Cancer Center

Lead Sponsor

N

National Cancer Institute (NCI)

Collaborating Sponsor

AI-Summary

What this Trial Is About

Researchers are evaluating how well the combination of cladribine, idarubicin, cytarabine, and quizartinib works and its side effects in treating adults with acute myeloid leukemia (AML) or high-risk myelodysplastic syndrome (MDS). This includes patients newly diagnosed, those whose disease has returned, or those whose disease does not respond to treatment. The study aims to understand the treatment's safety, effectiveness, and the genetic factors that may influence patient response. Participants receive treatment in three phases: induction, consolidation, and maintenance. During induction, patients get idarubicin, cladribine, and cytarabine intravenously on specific days, and quizartinib by mouth daily on days 6 to 19, repeated up to two cycles every 28 days if no disease progression or serious side effects occur. Those responding to induction move to consolidation with similar drugs on adjusted days and quizartinib daily on days 4 to 28 for up to five cycles. Maintenance involves daily quizartinib by mouth for up to 12 cycles, repeated every 28 days. Throughout the study, participants will be regularly monitored for treatment effects and side effects for up to 12 months, including evaluations of survival and disease status. After completing study treatment, follow-up visits occur every 6 to 12 months to assess long-term outcomes. Researchers will also study genetic changes and specific cell populations linked to treatment response, helping to understand how the combination affects the disease over time.

CONDITIONS

Brief Title

Cladribine, Idarubicin, Cytarabine, and Quizartinib in Treating Patients With Newly Diagnosed, Relapsed, or Refractory Acute Myeloid Leukemia or High-Risk Myelodysplastic Syndrome

Who Can Participate

Age: 18Years +
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Diagnosis of acute myeloid leukemia (AML) with 20% or more blasts, acute biphenotypic leukemia, or high-risk myelodysplastic syndrome (MDS) with more than 10% bone marrow blasts
  • Age 18 to 65 years for newly diagnosed patients; age 18 or older for relapsed patients
  • Newly diagnosed patients must not have received chemotherapy except limited use of hydroxyurea, tretinoin, or low-dose cytarabine for brief control
  • Relapsed or refractory patients with previously treated disease
  • Eastern Cooperative Oncology Group (ECOG) performance status of 2 or less
  • Creatinine level less than 1.5 mg/dL
  • Total bilirubin less than 1.5 mg/dL unless due to hemolysis or congenital disorder
  • Liver enzymes (SGPT) less than 2.5 times the upper limit of normal
  • Potassium, magnesium, and calcium levels within normal limits
  • Ability to take oral medication
  • Ability to understand and provide signed informed consent
  • Left ventricular ejection fraction at or above 50%
  • Women of childbearing potential must have a negative pregnancy test within 7 days and use contraception during and for 30 days after treatment; men must agree to use condoms if partner is of childbearing potential
  • Patients with isolated extramedullary myeloid neoplasm are eligible
Not Eligible

You will not qualify if you...

  • Any medical condition that may interfere with study procedures or results as judged by the treating physician
  • Breastfeeding women
  • Active malignancies or remission less than 6 months, except for certain skin cancers
  • Active serious infections with fever above 101°F within 48 hours before starting treatment
  • Significant gastrointestinal problems affecting quizartinib absorption
  • Active central nervous system leukemia (patients with previous CNS leukemia but no active disease are allowed)
  • Known HIV infection or active viral hepatitis
  • Major surgery within 14 days before starting study drug
  • Impaired heart function including abnormal ECG with QTc interval 450 milliseconds or more unless approved by medical monitor
  • History of congenital long QT syndrome or certain serious heart arrhythmias
  • Heart rate below 50 per minute on ECG
  • Certain heart conduction blocks unless patient has a pacemaker
  • Recent heart attack or unstable angina within 6 months
  • Severe congestive heart failure (NY Heart Association class III or IV)
  • Atrial fibrillation within 2 weeks before first dose
  • Use of strong CYP3A4 inducing medications active at study start

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Your Study Journey

Screening

Duration - 2 to 4 weeks

Participants are screened for eligibility to participate in the trial.

screening and enrollment visit

Treatment - Induction

Duration - Up to 2 cycles of 28 days each

Participants receive a combination of chemotherapy drugs including idarubicin, cladribine, cytarabine, and quizartinib to treat leukemia or high-risk myelodysplastic syndrome. This phase aims to induce remission.

Daily treatment during each 28-day cycle with intravenous infusions on specified days and oral medication daily on days 6-19

Treatment - Consolidation

Duration - Up to 5 cycles of 28 days each

Participants who achieve remission continue treatment with the same combination of drugs to consolidate response and prevent relapse.

Daily treatment during each 28-day cycle with intravenous infusions on specified days and oral medication daily on days 4-28

Treatment - Maintenance

Duration - Up to 12 cycles of 28 days each

Participants who maintain remission receive oral quizartinib daily to maintain response and prevent disease progression.

Daily oral medication during each 28-day cycle

Follow-up

Duration - Every 6 to 12 months after treatment ends

After treatment completion, participants are monitored regularly to assess their health and detect any disease recurrence.

Follow-up visits every 6 to 12 months

Trial Site Locations

Total: 1 location

1

M D Anderson Cancer Center

Houston, Texas, United States, 77030

Actively Recruiting

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Research Team

M

Musa Yilmaz

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NA

Model

SINGLE_GROUP

Primary Purpose

TREATMENT

Number of Arms

1

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