Actively Recruiting

All Genders
NCT04561518

ConTTRibute: A Global Observational Study of Patients With Transthyretin (TTR)-Mediated Amyloidosis (ATTR Amyloidosis)

Led by Alnylam Pharmaceuticals · Updated on 2026-03-31

1500

Participants Needed

40

Research Sites

509 weeks

Total Duration

On this page

AI-Summary

What this Trial Is About

The purpose of this study is to: * Describe epidemiological and clinical characteristics, natural history and real-world clinical management of ATTR amyloidosis patients * Characterize the safety and effectiveness of patisiran and vutrisiran as part of routine clinical practice in the real-world clinical setting * Describe disease emergence/progression in pre-symptomatic carriers of a known disease-causing transthyretin (TTR) variant

CONDITIONS

Official Title

ConTTRibute: A Global Observational Study of Patients With Transthyretin (TTR)-Mediated Amyloidosis (ATTR Amyloidosis)

Who Can Participate

All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Diagnosis of ATTR amyloidosis or documented known disease-causing TTR variant for the cohort of pre-symptomatic carriers
  • Germany Only: Patients must be treated per the summary of product characteristics (SmPC) for any approved treatment for ATTR amyloidosis
Not Eligible

You will not qualify if you...

  • Current enrollment in a clinical trial for any investigational agent

AI-Screening

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Trial Site Locations

Total: 40 locations

1

Clinical Trial Site

La Jolla, California, United States, 92037

Actively Recruiting

2

Clinical Trial Site

Los Angeles, California, United States, 90095

Actively Recruiting

3

Clinical Trial Site

Jacksonville, Florida, United States, 32224

Actively Recruiting

4

Clinical Trial Site

Iowa City, Iowa, United States, 52242

Actively Recruiting

5

Clinical Trial Site

Kansas City, Kansas, United States, 66160

Actively Recruiting

6

Clinical Trial Site

Baltimore, Maryland, United States, 21224

Actively Recruiting

7

Clinical Trial Site

Boston, Massachusetts, United States, 02127

Completed

8

Clinical Trial Site

New York, New York, United States, 10034

Actively Recruiting

9

Clinical Trial Site

Durham, North Carolina, United States, 27710

Actively Recruiting

10

Clinical Trial Site

Columbus, Ohio, United States, 43210

Actively Recruiting

11

Clinical Trial Site

Philadelphia, Pennsylvania, United States, 19104

Actively Recruiting

12

Clinical Trial Site

Austin, Texas, United States, 78756

Actively Recruiting

13

Clinical Trial Site

Houston, Texas, United States, 77030

Actively Recruiting

14

Clinical Trial Site

Salvador, Brazil

Actively Recruiting

15

Clinical Trial Site

São Paulo, Brazil

Actively Recruiting

16

Clinical Trial Site

Sofia, Bulgaria

Actively Recruiting

17

Clinical Trial Site

Aarhus, Denmark

Actively Recruiting

18

Clinical Trial Site

Copenhagen, Denmark

Completed

19

Clinical Trial Site

Bordeaux, France

Actively Recruiting

20

Clinical Trial Site

Bron, France

Actively Recruiting

21

Clinical Trial Site

Créteil, France

Actively Recruiting

22

Clinical Trial Site

Le Kremlin-Bicêtre, France

Actively Recruiting

23

Clinical Trial Site

Marseille, France

Actively Recruiting

24

Clinical Trial Site

Berlin, Germany

Actively Recruiting

25

Clinical Trial Site

Giessen, Germany

Actively Recruiting

26

Clinical Trial Site

Hanover, Germany

Actively Recruiting

27

Clinical Trial Site

Jerusalem, Israel

Actively Recruiting

28

Clinical Trial Site

Ramat Gan, Israel

Actively Recruiting

29

Clinical Trial Site

Milan, Italy

Actively Recruiting

30

Clinical Trial Site

Naples, Italy

Actively Recruiting

31

Clinical Trial Site

Palermo, Italy

Actively Recruiting

32

Clinical Trial Site

Roma, Italy

Actively Recruiting

33

Clinical Trial Site

Groningen, Netherlands

Actively Recruiting

34

Clinical Trial Site

Lisbon, Portugal

Actively Recruiting

35

Clinical Trial Site

Porto, Portugal

Actively Recruiting

36

Clinical Trial Site

Barcelona, Spain

Actively Recruiting

37

Clinical Trial Site

Madrid, Spain

Actively Recruiting

38

Clinical Trial Site

Palma, Spain

Actively Recruiting

39

Clinical Trial Site

New Taipei City, Taiwan

Actively Recruiting

40

Clinical Trial Site

Taipei, Taiwan

Actively Recruiting

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Research Team

A

Alnylam Clinical Trial Information Line

CONTACT

A

Alnylam Clinical Trial Information Line

CONTACT

How is the study designed?

Study Type

OBSERVATIONAL

Masking

N/A

Allocation

N/A

Model

N/A

Primary Purpose

N/A

Number of Arms

2

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