Actively Recruiting

Phase Not Applicable
Age: 10Years - 17Years
All Genders
ID06560736

Development of Novel Psychological Assessment Tools and Anxiety Intervention for PKU: Intervention Trial

Led by University of Missouri-Columbia · Updated on 2025-12-23

30

Participants Needed

1

Research Sites

N/A

Total Duration

On this page

Sponsors

U

University of Missouri-Columbia

Lead Sponsor

N

National PKU Alliance

Collaborating Sponsor

AI-Summary

What this Trial Is About

This research aims to evaluate a short-term skills-based intervention called Show Me FIRST for treating anxiety and depression in adolescents aged 10 to 17 with Phenylketonuria (PKU). The study also seeks to validate new psychological assessment tools that use ecological momentary assessment to capture real-time neurocognitive and psychological functions. Thirty adolescents with PKU and a history of anxiety or depression will take part in this randomized controlled trial. Participants will be randomly assigned to either an immediate intervention group or a wait-list/delayed intervention group, with each group receiving the 10-week Show Me FIRST program. The intervention and assessments are delivered remotely via secure videoconferencing and cell-phone applications, making participation accessible and convenient. During the study, participants will complete comprehensive psychological and cognitive evaluations at three timepoints: weeks 0, 11, and 22. These evaluations include various standardized scales and tests to measure anxiety, depression, executive function, attention, sleep, and blood phenylalanine levels. Researchers will closely monitor these outcomes to assess the intervention's impact and the validity of the assessment tools over the course of the study.

CONDITIONS

Brief Title

Development of Novel Psychological Assessment Tools and Anxiety Intervention for Phenylketonuria

Who Can Participate

Age: 10Years - 17Years
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Youth aged 10 to 17 years with a parent or guardian
  • Formal diagnosis of PKU confirmed by newborn screening with blood phenylalanine level 60 bcmol/L
  • Received PKU treatment within the first 30 days of life
  • Interested in a brief psychotherapeutic program for anxiety and/or depression symptoms
  • Located in Missouri, Kansas, or Illinois
Not Eligible

You will not qualify if you...

  • Significant intellectual disability (IQ less than 70) or language difficulties interfering with psychotherapy
  • Plans to receive psychotherapy outside the study during participation
  • Plans to change current psychoactive or PKU-related medication during participation
  • Active suicidal thoughts requiring immediate or higher-level care

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Your Study Journey

Screening

Duration - 2 to 4 weeks

Participants are screened for eligibility to participate in the trial.

1 visit (remote)

Outpatient Treatment

Duration - 10 weeks

Participants receive the 10-week Show Me FIRST coping skills intervention for anxiety and depression delivered remotely via secure videoconference and phone applications.

Weekly remote sessions

Follow-up

Duration - Up to 22 weeks

Participants complete psychological and neurocognitive evaluations at Weeks 0, 11, and 22 to assess treatment outcomes remotely.

3 remote assessment visits

Trial Site Locations

Total: 1 location

1

University of Missouri

Columbia, Missouri, United States, 65201

Actively Recruiting

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Research Team

S

Shawn Christ

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

RANDOMIZED

Model

PARALLEL

Primary Purpose

TREATMENT

Number of Arms

2

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