Actively Recruiting
DMD Voice: Qualitative Interviews With Patients and Caregivers
Led by Red Nucleus Enterprise Solutions, LLC · Updated on 2025-04-30
68
Participants Needed
1
Research Sites
87 weeks
Total Duration
On this page
Sponsors
R
Red Nucleus Enterprise Solutions, LLC
Lead Sponsor
I
Italfarmaco S.A
Collaborating Sponsor
AI-Summary
What this Trial Is About
The purpose of this study is to understand DMD functional losses or abilities and their association with independence and quality of life from the perspective of individuals with DMD and/or and their caregivers. This is a qualitative interview study in which individuals with DMD and/or their caregivers will be asked to participate in a semi-structured, approximately 60- minute interview. Interviews will focus on functional abilities and independence. Caregivers and boys with DMD will be interviewed. This study includes no treatment nor intervention; however, some participants are being treated by a drug that is approved in the U.S. and the U.K. and under investigation in other geographies.
CONDITIONS
Official Title
DMD Voice: Qualitative Interviews With Patients and Caregivers
Who Can Participate
Eligibility Criteria
You may qualify if you...
- Patients must have been treated with givinostat for at least 2 years
- Patients must be at least 10 years old with signed consent from a parent or legal guardian
- Patients must be currently taking givinostat
- Patients must be willing and able to participate in a video or audio recorded interview
- Caregivers must be a parent or legal guardian of an individual with DMD treated with givinostat for at least 2 years
- Caregivers must be willing and able to participate in a video or audio recorded interview
- Caregivers must provide care to an individual with DMD who cannot raise their hands above their head
- Caregivers must reside in the United States or Canada
- Caregivers must be able to read, speak, and understand English
- Caregivers must be willing and able to participate in a video or audio recorded interview
- Caregivers must have access to a stable internet connection
You will not qualify if you...
History of severe allergic reactions to study medication Currently pregnant or breastfeeding Recent participation in another clinical trial within the last 30 days Presence of uncontrolled medical conditions that could affect safety
AI-Screening
AI-Powered Screening
Complete this quick 3-step screening to check your eligibility
Trial Site Locations
Total: 1 location
1
Red Nucleus
Yardley, Pennsylvania, United States, 19067
Actively Recruiting
Research Team
M
Mary Hubbard
CONTACT
How is the study designed?
Study Type
OBSERVATIONAL
Masking
N/A
Allocation
N/A
Model
N/A
Primary Purpose
N/A
Number of Arms
3
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