Actively Recruiting
Dose Finding Study to Evaluate the Safety of BSB-2002 in Relapsed or Refractory Acute Myeloid Leukemia (AML) Patients With NPM1 Mutation
Led by BlueSphere Bio, Inc · Updated on 2026-05-05
19
Participants Needed
1
Research Sites
71 weeks
Total Duration
On this page
AI-Summary
What this Trial Is About
The goal of this clinical trial is to test BSB-2002 which is a new type of cellular therapy to treat blood cancer (AML). It will evaluate the safety of BSB-2002 and also determine whether it works to prevent relapse of your cancer.
CONDITIONS
Official Title
Dose Finding Study to Evaluate the Safety of BSB-2002 in Relapsed or Refractory Acute Myeloid Leukemia (AML) Patients With NPM1 Mutation
Who Can Participate
Eligibility Criteria
You may qualify if you...
- Male or female patients aged 18 years or older
- Diagnosed with AML per ELN criteria and treated with at least two lines of therapy
- AML is relapsed (after previous remission) or refractory to last treatment
- MRD positive by NGS for NPM1 after previously being MRD negative
- HLA-A*02:01 positive
- Positive for NPM1 mutation type A, D, G, or H
- Adequate venous access for apheresis or agree to central line use
- Willing and able to provide informed consent and follow study requirements
You will not qualify if you...
- Leukemic blast count above 20,000/µl unless controlled with hydroxyurea
- AML with only extramedullary involvement
- Candidates for hematopoietic stem cell transplant
- Eligible to receive approved targeted therapy
- Use of other investigational agents within 5 half-lives before dosing
- Hematopoietic stem cell transplant within 3 months or with significant graft-versus-host disease or persistent Grade 2+ toxicity
- Other malignancies requiring treatment
- Uncontrolled bacterial, viral, or fungal infections
- Active Hepatitis B or C infection
- HIV-1 or HIV-2 positive
- CNS involvement refractory to treatment
- Congestive heart failure NYHA class 3 or 4 or recent history without adequate heart function
- Renal insufficiency with creatinine clearance below 40 ml/min/1.73m2 or serum creatinine above 1.6 mg/dL
- Total bilirubin more than twice the upper limit of normal unless due to Gilbert's Syndrome
- AST or ALT more than three times the upper limit of normal
- Pregnant or lactating women
- ECOG performance status greater than 2
- Ongoing treatment with chronic immunosuppressants
- Women of childbearing potential and fertile men unwilling to use effective birth control or abstinence for 12 months
- Any condition that may interfere with participation or study data interpretation as judged by the Investigator
AI-Screening
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Trial Site Locations
Total: 1 location
1
Washington University at St Louis
St Louis, Missouri, United States, 63110
Actively Recruiting
Research Team
M
Medical Director: Nawazish Khan, BlueSphere Bio, MD
CONTACT
How is the study designed?
Study Type
INTERVENTIONAL
Masking
NONE
Allocation
NON_RANDOMIZED
Model
SEQUENTIAL
Primary Purpose
TREATMENT
Number of Arms
2
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