Actively Recruiting

Phase 3
Age: 7Years - 21Years
All Genders
NCT05230758

Effect of Metformin on Behaviour and the Brain in Children Treated for a Brain Tumour

Led by Donald Mabbott · Updated on 2026-05-01

140

Participants Needed

20

Research Sites

282 weeks

Total Duration

On this page

AI-Summary

What this Trial Is About

The efficacy of treatment with metformin for promoting cognitive recovery and brain growth in children/adolescents treated for a brain tumour will be investigated in a multi-site Phase III randomized double-blind placebo-controlled parallel arm superiority trial. Specifically, in children/adolescents aged 7 years to 21 years and 11 months who have completed treatment for a brain tumour, is oral administration of metformin for 16 weeks associated with greater improvement of cognitive function and brain growth compared to placebo administered for 16 weeks?

CONDITIONS

Official Title

Effect of Metformin on Behaviour and the Brain in Children Treated for a Brain Tumour

Who Can Participate

Age: 7Years - 21Years
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • At least 3 weeks post completion of primary therapy for medulloblastoma, ependymoma, craniopharyngioma, germ cell tumours, or other brain tumours treated with cranial radiation, or cranial radiation for relapsed ependymoma
  • Aged between 7 years and 21 years 11 months at enrollment
  • Native English or French speaker, or at least two years of schooling in English or French
  • Able and willing to swallow tablets whole, crushed, or via feeding tube and adhere to the treatment regimen
  • Normal kidney function with estimated glomerular filtration rate (eGFR) over 75 ml/min/1.73m²
  • Normal liver function with specific limits for AST, ALT, and total bilirubin levels
  • Provided informed consent and assent if applicable
Not Eligible

You will not qualify if you...

  • Full scale IQ score below 60 on Wechsler intelligence scales at screening
  • Known allergy to metformin hydrochloride
  • Unstable or insulin-dependent (Type 1) diabetes
  • History of hypoglycemia after age 2
  • Diagnosis of acute or chronic metabolic or lactic acidosis, or low bicarbonate levels at screening
  • History of kidney disease before brain tumour diagnosis
  • History of congestive heart failure requiring treatment within 2 years prior to study
  • Currently in a cognitive rehabilitation study
  • Treatment with or planned use of diuretics or certain kidney-excreted cationic drugs
  • Treatment with medications that may interact with metformin including lamotrigine, beta blockers, ACE inhibitors, glycopyrrolate, carbonic anhydrase inhibitors, or others at investigator discretion
  • Pernicious anemia at screening
  • Current use of metformin
  • Any condition that may interfere with study compliance or safety as judged by investigators
  • Receiving palliative care

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Trial Site Locations

Total: 20 locations

1

John Hunter Children's Hospital

New Lambton Heights, New South Wales, Australia, 2305

Actively Recruiting

2

Children's Hospital in Westmead

Westmead, New South Wales, Australia, 2145

Withdrawn

3

Women and Childen's Hospital

Adelaide, North Adelaide, Australia, SA 5006

Actively Recruiting

4

Monash Children's Hospital

Clayton, Victoria, Australia, 3168

Actively Recruiting

5

Royal Children's Hospital

Parkville, Victoria, Australia, 3052

Actively Recruiting

6

Perth Children's Hospital

Nedlands, Western Australia, Australia, 6009

Actively Recruiting

7

Alberta Children's Hospital

Calgary, Alberta, Canada, T3B 6A8

Actively Recruiting

8

Stollery Children's Hospital

Edmonton, Alberta, Canada, T6G 2B7

Actively Recruiting

9

Children's & Women's Health Centre of British Columbia

Vancouver, British Columbia, Canada, V6H 3V4

Actively Recruiting

10

Cancer Care Manitoba

Winnipeg, Manitoba, Canada, R3E 0V9

Actively Recruiting

11

Izaak Walton Killam (IWK) Health Centre

Halifax, Nova Scotia, Canada, B3K 6R8

Actively Recruiting

12

Hamilton Health Sciences - McMaster Children's Hospital

Hamilton, Ontario, Canada, L8S 4K1

Actively Recruiting

13

Children's Hospital, London Health Sciences Centre

London, Ontario, Canada, N6A 5W9

Actively Recruiting

14

Children's Hospital of Eastern Ontario

Ottawa, Ontario, Canada, K1H 8L1

Actively Recruiting

15

The Hospital for Sick Children

Toronto, Ontario, Canada, M5G 1X8

Actively Recruiting

16

CHU Sainte-Justine

Montreal, Quebec, Canada, H3T 1C5

Actively Recruiting

17

Montreal Children's Hospital

Montreal, Quebec, Canada, H4A 3J1

Actively Recruiting

18

CHU de Québec - Université Laval

Québec, Quebec, Canada, G1V 4G2

Actively Recruiting

19

CHU de Sherbrooke

Sherbrooke, Quebec, Canada, J1G 2E8

Actively Recruiting

20

Saskatchewan Health Authority

Saskatoon, Saskatchewan, Canada, S7N 0W8

Actively Recruiting

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Research Team

L

Lauren Cole, PhD

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

QUADRUPLE

Allocation

RANDOMIZED

Model

PARALLEL

Primary Purpose

SUPPORTIVE_CARE

Number of Arms

2

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